Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2026-04-20

Clinical Trial Update: Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency

View source ↗

Summary

Expanded access program update for tiratricol in patients with Monocarboxylate Transporter 8 deficiency (Allan-Herndon-Dudley Syndrome).

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • tiratricol (tiratricol)

Snippet

Sponsor: Rare Thyroid Therapeutics International AB | Conditions: Monocarboxylate Transporter 8 Deficiency, Allan-Herndon-Dudley Syndrome | Status: AVAILABLE