CLINICAL_TRIALS
research
· 2026-04-20
Clinical Trial Update: Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency
Summary
Expanded access program update for tiratricol in patients with Monocarboxylate Transporter 8 deficiency (Allan-Herndon-Dudley Syndrome).
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Rare Thyroid Therapeutics International AB | Conditions: Monocarboxylate Transporter 8 Deficiency, Allan-Herndon-Dudley Syndrome | Status: AVAILABLE