Menkes Disease
📧 Sign up to get email alerts when something new happens for Menkes Disease.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-04-13Clinical Trial Update: NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn Syndrome [Phase 1, Phase 2]
Phase 1/2 study of droxidopa (NORTHERA) for autonomic dysfunction in adult survivors of Menkes disease and occipital horn syndrome has compl…
-
CLINICAL_TRIALS trial_result · 2026-03-02Clinical Trial Update: Long Term Follow-up on Menkes Disease Patients
A clinical trial update reports long-term follow-up data for Menkes disease patients enrolled in a Sentynl Therapeutics study; the trial is …
-
CLINICAL_TRIALS trial_result · 2020-11-19Clinical Trial Update: Molecular Bases of Response to Copper Treatment in Menkes Disease, Related Phenotypes, and Unexplained Copper Deficiency [Phase 3]
Phase 3 trial update on copper treatment in Menkes disease, related phenotypes, and unexplained copper deficiency.
-
CLINICAL_TRIALS trial_result · 2015-10-30Clinical Trial Update: Copper Histidine Therapy for Menkes Diseases [Phase 1, Phase 2]
This clinical trial update reports on Phase 1 and Phase 2 evaluation of copper histidine therapy for Menkes disease (kinky hair syndrome), w…