Clinical Trial Update: NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn Syndrome [Phase 1, Phase 2]

View source ↗

Summary

Phase 1/2 study of droxidopa (NORTHERA) for autonomic dysfunction in adult survivors of Menkes disease and occipital horn syndrome has completed enrollment, and…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Menkes Disease
• Occipital Horn Syndrome

Drugs mentioned

• Northera (droxidopa)

Snippet

Sponsor: Stephen G. Kaler, MD | Conditions: Menkes Disease, Occipital Horn Syndrome | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2026-04-13