Menkes Disease
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CLINICAL_TRIALS research · 2026-02-10Clinical Trial Update: Phase I/II Study of NORTHERA (DROXIDOPA) for Dysautonomia in Pediatric Survivors of Menkes Disease. [Phase 1, Phase 2]
Phase I/II study of droxidopa (NORTHERA) for dysautonomia in pediatric survivors of Menkes disease is currently recruiting.