Menkes Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-04-13Clinical Trial Update: NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn Syndrome [Phase 1, Phase 2]
Phase 1/2 study of droxidopa (NORTHERA) for autonomic dysfunction in adult survivors of Menkes disease and occipital horn syndrome has compl…
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CLINICAL_TRIALS approval · 2026-03-02Clinical Trial Update: Copper Histidinate Treatment for Menkes Disease
Copper histidinate has been approved for marketing to treat Menkes disease.
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CLINICAL_TRIALS trial_result · 2026-03-02Clinical Trial Update: Long Term Follow-up on Menkes Disease Patients
A clinical trial update reports long-term follow-up data for Menkes disease patients enrolled in a Sentynl Therapeutics study; the trial is …
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CLINICAL_TRIALS research · 2026-02-10Clinical Trial Update: Phase I/II Study of NORTHERA (DROXIDOPA) for Dysautonomia in Pediatric Survivors of Menkes Disease. [Phase 1, Phase 2]
Phase I/II study of droxidopa (NORTHERA) for dysautonomia in pediatric survivors of Menkes disease is currently recruiting.
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FDA approval · 2026-01-12FDA Approved: ZYCUBO — Original Application (Sentynl Therapeutics, Inc.)
FDA approved ZYCUBO (copper histidinate) in an original application from Sentynl Therapeutics for treatment of copper deficiency associated …
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CLINICAL_TRIALS trial_result · 2020-11-19Clinical Trial Update: Molecular Bases of Response to Copper Treatment in Menkes Disease, Related Phenotypes, and Unexplained Copper Deficiency [Phase 3]
Phase 3 trial update on copper treatment in Menkes disease, related phenotypes, and unexplained copper deficiency.
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CLINICAL_TRIALS trial_result · 2015-10-30Clinical Trial Update: Copper Histidine Therapy for Menkes Diseases [Phase 1, Phase 2]
This clinical trial update reports on Phase 1 and Phase 2 evaluation of copper histidine therapy for Menkes disease (kinky hair syndrome), w…