Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2025-04-01Clinical Trial Update: Haemophilia and Bone Loss - PHILEOS Study [NA]
This document provides a status update on the PHILEOS clinical trial investigating bone loss in people with hemophilia, which is currently r…
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CLINICAL_TRIALS withdrawal · 2025-03-11Clinical Trial Update: A Study of SerpinPC in Participants with Hemophilia B (HemB) with Inhibitors [Phase 2]
A Phase 2 study of SerpinPC in participants with Hemophilia B with inhibitors has been terminated.
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CLINICAL_TRIALS trial_result · 2025-03-11Clinical Trial Update: The Efficacy and Safety of SerpinPC in Participants with Severe Hemophilia a or Moderately Severe to Severe Hemophilia B [Phase 2]
Phase 2 trial evaluating the efficacy and safety of SerpinPC in participants with severe Hemophilia A or moderately severe to severe Hemophi…
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EMA approval · 2025-03-07EMA Authorised: BeneFIX (nonacog alfa) — Pfizer Europe MA EEIG
The European Medicines Agency authorised BeneFIX (nonacog alfa) for Hemophilia B.
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EMA approval · 2025-03-05EMA Authorised: ReFacto AF (moroctocog alfa) — Pfizer Europe MA EEIG
The European Medicines Agency authorised ReFacto AF (moroctocog alfa) for the treatment of Hemophilia A. Decision date: 03/03/2025.
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CLINICAL_TRIALS research · 2025-03-05Clinical Trial Update: Gene Therapy for Haemophilia A. [Phase 1, Phase 2]
This is an update on an ongoing Phase 1/2 gene therapy trial for Hemophilia A sponsored by University College London, currently not recruiti…
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CLINICAL_TRIALS research · 2025-02-24Clinical Trial Update: Chronic Pain and Hemophilia
A clinical trial update indicates a study sponsored by University Hospital, Clermont-Ferrand is currently recruiting participants for condit…
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CLINICAL_TRIALS research · 2025-02-24Clinical Trial Update: The Efficacy and Safety of ZS801 in Chinese Hemophilia B Patients. [NA]
This entry reports on the ongoing clinical trial evaluating the efficacy and safety of ZS801 in Chinese patients with Hemophilia B. Recruitm…
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CLINICAL_TRIALS research · 2025-02-24Clinical Trial Update: A Study to Evaluate the Safety and Efficacy of ZS801 in Adult Hemophilia B Patients [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating the safety and efficacy of ZS801 in adult Hemophilia B patients is currently recruiting.
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CLINICAL_TRIALS research · 2025-02-21Clinical Trial Update: Gene Therapy for Hemophilia B Patients Aged 12-18 Years Old [Phase 1]
A Phase 1 clinical trial of a gene therapy for Hemophilia B in patients aged 12-18 is currently recruiting.
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CLINICAL_TRIALS research · 2025-02-21Clinical Trial Update: Safety and Tolerability of VGB-R04 in Patients With Haemophilia B [EARLY_Phase 1]
An early-phase, safety and tolerability study of VGB-R04 in Hemophilia B is currently recruiting.
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CLINICAL_TRIALS research · 2025-02-21Clinical Trial Update: Safety and Efficacy Study of NGGT003 in Hemophilia A Patients [EARLY_Phase 1]
An early Phase 1 trial is evaluating the safety and efficacy of NGGT003 in patients with Hemophilia A. The study is currently recruiting.
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CLINICAL_TRIALS trial_result · 2025-02-21Clinical Trial Update: Gene Therapy for Chinese Hemophilia B [NA]
A completed clinical trial in China studied a gene therapy approach for Hemophilia B.
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CLINICAL_TRIALS trial_result · 2025-02-21Clinical Trial Update: The Efficacy and Safety of ZS802 in Chinese Hemophilia A Patients. [NA]
This clinical trial update reports on the efficacy and safety of ZS802 for Hemophilia A in Chinese patients; the study is currently recruiti…
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CLINICAL_TRIALS research · 2025-02-21Clinical Trial Update: A Study of FVIII Gene Therapy for Hemophilia A [EARLY_Phase 1]
A Phase I study investigating Factor VIII gene therapy for Hemophilia A is currently recruiting in China.
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CLINICAL_TRIALS trial_result · 2025-02-13Clinical Trial Update: Safety and Pharmacokinetics of Subcutaneous Injection of OCTA101 in Adult Patients With Severe Hemophilia A [Phase 1, Phase 2]
Phase 1/2 trial evaluating safety and pharmacokinetics of subcutaneous OCTA101 in adults with Hemophilia A; the study was terminated but res…
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CLINICAL_TRIALS research · 2025-02-13Clinical Trial Update: Comparison of Upper Extremity Functional Performance in Hemophilic and Healthy Children
A study is currently enrolling by invitation to compare upper-extremity functional performance between children with hemophilia and healthy …
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CLINICAL_TRIALS trial_result · 2025-02-12Clinical Trial Update: ATHN 7: Hemophilia Natural History Study
ATHN 7 is a natural history study of hemophilia patients conducted by the American Thrombosis and Hemostasis Network, and this update notes …
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CLINICAL_TRIALS research · 2025-02-10Clinical Trial Update: Cartilage Biomarkers and HEAD-US Score in Severe Hemophilia A Patients Receiving FVIII Prophylaxis [NA]
An update on cartilage biomarkers and HEAD-US ultrasound scores in patients with severe Hemophilia A receiving Factor VIII prophylaxis.
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CLINICAL_TRIALS trial_result · 2025-02-10Clinical Trial Update: The Long-term Safety and Efficacy of SerpinPC in Subjects with Hemophilia Who Completed a Sponsored SerpinPC Clinical Trial [Phase 3]
This clinical trial update covers the long-term safety and efficacy of SerpinPC in people with Hemophilia A or Hemophilia B who completed pr…
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CLINICAL_TRIALS research · 2025-02-10Clinical Trial Update: Manual Therapy in Hemophilic Arthropathy of the Ankle [NA]
This clinical trial is evaluating manual therapy for hemophilic arthropathy of the ankle in people with Hemophilia A; recruitment is ongoing…
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CLINICAL_TRIALS trial_result · 2025-02-07Clinical Trial Update: Hemophilia Non-Interventional Study Prior to SerpinPC Intervention (PRESent-5)
A non-interventional study in Hemophilia A and Hemophilia B evaluating eligibility before SerpinPC treatment has been terminated.
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CLINICAL_TRIALS trial_result · 2025-02-06Clinical Trial Update: The Safety and Tolerability of SerpinPC in Healthy Men and in Men with Severe Blood Disorders (haemophilia a and B) [Phase 1, Phase 2]
The trial update reports on the safety and tolerability of SerpinPC in healthy men and in men with Hemophilia A or B across Phase 1 and Phas…
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CLINICAL_TRIALS research · 2025-02-05Clinical Trial Update: Synovial Proliferation on Routine Ultrasound: Active or Inactive?
A clinical trial evaluating synovial proliferation in hemophilia patients using routine ultrasound is not yet recruiting.
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CLINICAL_TRIALS trial_result · 2025-02-04Clinical Trial Update: ADYNOVATE Drug Use-Results Survey
Takeda released results from a Hemophilia A drug-use survey of ADYNOVATE. The results were posted on February 4, 2025.