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CLINICAL_TRIALS research · 2025-02-21

Clinical Trial Update: Gene Therapy for Hemophilia B Patients Aged 12-18 Years Old [Phase 1]

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Summary

A Phase 1 clinical trial of a gene therapy for Hemophilia B in patients aged 12-18 is currently recruiting.

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Diseases / indications

Snippet

Sponsor: Institute of Hematology & Blood Diseases Hospital, China | Conditions: Hemophilia B | Phase 1 | Status: RECRUITING