Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-01-22Clinical Trial Update: Safety and Efficacy of STSP-0601 in Adult Patients with Hemophilia a or B with Inhibitor [Phase 2]
A Phase 2 study evaluating the safety and efficacy of STSP-0601 in adults with Hemophilia A or B with inhibitors has completed.
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CLINICAL_TRIALS trial_result · 2025-01-20Clinical Trial Update: Factor IX as Adjunctive Therapy to Emicizumab (EMIX) [EARLY_Phase 1]
This is an early Phase 1 study evaluating Factor IX as adjunctive therapy to Emicizumab (EMIX) for Hemophilia A. The trial status shows comp…
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CLINICAL_TRIALS trial_result · 2025-01-16Clinical Trial Update: An 18-month Low-interventional Study to Assess Joint Health in Haemophilia A and B Patients on Prophylaxis With Efmoroctocog Alfa or Eftrenonacog Alfa [Phase 4]
This update reports the termination of an 18-month Phase 4 study evaluating joint health in haemophilia A and B patients on prophylaxis with…
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CLINICAL_TRIALS research · 2025-01-14Clinical Trial Update: Measurement Properties in People with Hemophilia [NA]
Status indicates recruiting for a University of Zurich study evaluating measurement properties in people with Hemophilia A and Hemophilia B.
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CLINICAL_TRIALS trial_result · 2025-01-13Clinical Trial Update: EVALUATION of the OVERALL HAEMOSTATIC CAPACITY of MIM8 with GLOBAL HAEMOSTASIS ASSAYS and FIBRIN CLOT ULTRASTRUCTURE
A completed clinical trial evaluating the overall haemostatic capacity of MIM8 using global haemostasis assays and fibrin clot ultrastructur…
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CLINICAL_TRIALS trial_result · 2024-12-30Clinical Trial Update: A Gene Transfer Study for Hemophilia A [Phase 1, Phase 2]
Clinical trial update for a gene transfer therapy in Hemophilia A (Phase 1/2) with completed status and results posted.
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CLINICAL_TRIALS trial_result · 2024-12-30Clinical Trial Update: KN057 Multiple Dose Study in Moderately Severe to Severe Hemophilia [Phase 2]
A Phase 2 multiple-dose study of KN057 in moderately severe to severe hemophilia has completed, with the update noting trial status rather t…
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CLINICAL_TRIALS research · 2024-12-24Clinical Trial Update: KN057 Multiple Dose Study in Patients with Hemophilia a or Hemophilia B with or Without Inhibitors [Phase 2]
Phase 2 multiple-dose study of KN057 in patients with Hemophilia A or Hemophilia B (with or without inhibitors) is not yet recruiting.
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FDA approval · 2024-12-20FDA Approved: ALHEMO — Original Application (Novo Nordisk)
The FDA approved ALHEMO (concizumab) from Novo Nordisk based on the original application, intended to prevent bleeding episodes in patients …
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CLINICAL_TRIALS research · 2024-12-20Clinical Trial Update: Liver Biopsy In Haemophilia Gene Therapy [NA]
A clinical trial update indicates a liver biopsy component is being evaluated in a haemophilia gene therapy study, with patient recruitment …
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EMA approval · 2024-12-19EMA Authorised: Idelvion (albutrepenonacog alfa) — CSL Behring GmbH
The European Medicines Agency authorised Idelvion (albutrepenonacog alfa) by CSL Behring for Hemophilia B, marking EU marketing approval; it…
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EMA approval · 2024-12-18EMA Authorised: Voncento (human coagulation factor VIII;human von willebrand factor) — CSL Behring GmbH
The EMA authorised Voncento, a Factor VIII/von Willebrand factor concentrate by CSL Behring, for treatment of Hemophilia A and von Willebran…
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CLINICAL_TRIALS research · 2024-12-18Clinical Trial Update: An Open-label Study Evaluating the Efficacy, Safety, Pharmacokinetics, and Immunogenicity of SKP-0141 for the Treatment and Prophylaxis in Severe Hemophilia a Patients [Phase 3]
Open-label Phase 3 trial evaluating SKP-0141 for treatment and prophylaxis in severe Hemophilia A, assessing efficacy, safety, pharmacokinet…
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CLINICAL_TRIALS withdrawal · 2024-12-13Clinical Trial Update: Study of a Gene Therapy Treatment for Hemophilia A [Phase 3]
A Phase 3 gene therapy trial for Hemophilia A sponsored by Spark Therapeutics has been withdrawn.
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CLINICAL_TRIALS research · 2024-12-11Clinical Trial Update: Longitudinal Cohort of Thrombosis and Hemostasis Diseases
A longitudinal cohort clinical trial in China studying thrombosis and hemostasis diseases. It is currently recruiting at Peking University P…
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EMA approval · 2024-12-05EMA Authorised: Esperoct (turoctocog alfa pegol) — Novo Nordisk A/S
EMA authorised Esperoct (turoctocog alfa pegol) from Novo Nordisk A/S for the treatment of hemophilia A. The decision date was 21 October 20…
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CLINICAL_TRIALS trial_result · 2024-11-29Clinical Trial Update: Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A
This update summarizes long-term safety and efficacy data from Spark Therapeutics–sponsored gene therapies studied in males with Hemophilia …
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EMA approval · 2024-11-27EMA Authorised: Rixubis (nonacog gamma) — Baxalta Innovations GmbH
The European Medicines Agency authorised Rixubis (nonacog gamma) by Baxalta Innovations GmbH for the treatment of Hemophilia B.
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CLINICAL_TRIALS trial_result · 2024-11-27Clinical Trial Update: In Vitro Correction of Thrombin Generation by Concizumab (Anti-TFPI) for Severe Hemophilia Patients
This completed trial update reports in vitro evidence that concizumab (an anti-TFPI antibody) corrected thrombin generation in samples from …
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CLINICAL_TRIALS research · 2024-11-25Clinical Trial Update: Home Monitoring in Hemophilia a
This study from Radboud University Medical Center is exploring home monitoring for patients with Hemophilia A. The trial is currently recrui…
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CLINICAL_TRIALS trial_result · 2024-11-15Clinical Trial Update: A Study of TAK-660 in Surgical Procedures for People With Hemophilia A.
TAK-660 has completed a study evaluating its use in surgical procedures for people with Hemophilia A, with results posted on 2024-11-15.
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CLINICAL_TRIALS trial_result · 2024-10-29Clinical Trial Update: Case and Use Scenario Study to Gain Knowledge on the User Needs for a Medical Device for Hemophilia a Monitoring
This completed clinical trial conducted case and use scenario studies to gather insights on user needs for a medical device intended to moni…
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CLINICAL_TRIALS trial_result · 2024-10-21Clinical Trial Update: Effect of Kinetic Chain Exercises on Muscle Strength, Joint Position Sense and Quality of Life in Children with Haemophilia. [NA]
A clinical trial investigating how kinetic chain exercises affect muscle strength, joint position sense, and quality of life in children wit…
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CLINICAL_TRIALS trial_result · 2024-10-02Clinical Trial Update: Prospective, Non-interventional Study to Evaluate the Effectiveness of Elocta Compared to Conventional Factor Products
A completed non-interventional study comparing the effectiveness of Elocta with conventional factor VIII products in individuals with Hemoph…
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CLINICAL_TRIALS trial_result · 2024-09-27Clinical Trial Update: Study of TU7710 in Warfarin Anti-coagulated Healthy Male Subjects [Phase 1]
Phase 1 study evaluating TU7710 in warfarin-anticoagulated healthy male subjects; conditions listed include Hemophilia A and Hemophilia B.