Hemophilia
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CLINICAL_TRIALS other · 2025-09-05Clinical Trial Update: Treatment of Hemophilia A Patients With FVIII Inhibitors
The update announces an ongoing clinical trial for Hemophilia A patients with factor VIII inhibitors that is currently recruiting. It does n…
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CLINICAL_TRIALS research · 2025-09-02Clinical Trial Update: Global Haemostatic Methods Following Administration of Bypassing Agents to Patients With Haemophilia With Inhibitors
Karolinska Institutet is conducting a trial to study global haemostatic methods following administration of bypassing agents in patients wit…
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CLINICAL_TRIALS research · 2025-08-29Clinical Trial Update: Post-marketing Surveillance (Special Use-results Surveillance) on Treatment With Alhemo
This document describes a post-marketing surveillance clinical trial of Alhemo for Hemophilia A and Hemophilia B, sponsored by Novo Nordisk …
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CLINICAL_TRIALS withdrawal · 2025-08-29Clinical Trial Update: Patient Interview Study to Explore the Impact of Gene Therapy in Hemophilia A & B
Pfizer-sponsored clinical trial assessing gene therapy for Hemophilia A and Hemophilia B has been withdrawn from clinicalTrials.gov.
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FDA approval · 2025-08-27FDA Approved: DESMOPRESSIN ACETATE — Supplemental Application (Avenacy, Inc.)
FDA approved a supplemental application for Desmopressin Acetate by Avenacy, Inc.
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CLINICAL_TRIALS research · 2025-08-26Clinical Trial Update: Study of AAV5-hFIX in Severe or Moderately Severe Haemophilia B
This clinical trial update indicates CSL Behring's AAV5-hFIX gene therapy trial for Hemophilia B is currently active but not recruiting.
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CLINICAL_TRIALS research · 2025-08-22Clinical Trial Update: Patient Reported Outcomes Burdens and Experiences - Phase 3
Phase 3 clinical trial update focusing on patient-reported outcomes burdens and experiences is currently recruiting. The study involves cond…
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CLINICAL_TRIALS trial_result · 2025-08-22Clinical Trial Update: Gene Therapy Study in Severe Hemophilia A Patients With Antibodies Against AAV5 [Phase 1, Phase 2]
BioMarin's Phase 1/2 gene therapy trial in severe Hemophilia A patients with antibodies against AAV5 was terminated and results have been po…
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CLINICAL_TRIALS research · 2025-08-21Clinical Trial Update: Examination of Physiotherapists' Knowledge, Awareness and Competence on Physical Activity and Exercise in Hemophilia Patients
This clinical trial update examines physiotherapists' knowledge, awareness, and competence regarding physical activity and exercise in peopl…
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CLINICAL_TRIALS research · 2025-08-19Clinical Trial Update: Topical and Local TXA in Facelifts - A Randomized Controlled Double Blinded Study [EARLY_Phase 1]
A randomized, double-blind Phase 1 trial evaluating topical and local tranexamic acid to reduce bleeding during facelift surgery, currently …
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CLINICAL_TRIALS trial_result · 2025-08-17Clinical Trial Update: Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults [Phase 3]
Pfizer is evaluating the efficacy and safety of giroctocogene fitelparvovec (PF-07055480) gene therapy in adults with moderately severe to s…
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CLINICAL_TRIALS trial_result · 2025-08-17Clinical Trial Update: Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults [Phase 3]
Phase 3 trial update for PF-07055480 Giroctocogene fitelparvovec gene therapy in adults with moderately severe to severe Hemophilia A.
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CLINICAL_TRIALS other · 2025-08-15Clinical Trial Update: Version Testing of EnzySystem Version A for Hemophilia A
A clinical trial (NCT06273865) evaluating EnzySystem Version A for Hemophilia A is currently suspended, per Radboud University Medical Cente…
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CLINICAL_TRIALS trial_result · 2025-08-12Clinical Trial Update: Effects of Ultrasound and Infrared on Joint Pain and Movement in Hemophilia A Patients. [NA]
This completed clinical trial evaluated whether ultrasound and infrared therapy can reduce joint pain and improve movement in people with He…
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CLINICAL_TRIALS other · 2025-08-11Clinical Trial Update: He-move-philia, Lifestyle Intervention for Patients With Hemophilia [NA]
A clinical trial update for a lifestyle intervention study in patients with hemophilia, currently active but not recruiting.
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CLINICAL_TRIALS trial_result · 2025-08-08Clinical Trial Update: Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B [Phase 3]
Phase 3 trial status update for Fitusiran prophylaxis in male pediatric patients aged 1 to less than 12 years with Hemophilia A or B; the st…
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CLINICAL_TRIALS research · 2025-08-05Clinical Trial Update: Association of Prophylactic Treatment With Treatment Burden and Psychosocial Variables in Patients With Hemophilia
A clinical trial is currently recruiting to study the association between prophylactic treatment and treatment burden and psychosocial facto…
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CLINICAL_TRIALS research · 2025-08-03Clinical Trial Update: Data Registry in Chinese Hemophilia A and B Patients
A completed data registry study conducted in China for patients with Hemophilia A and Hemophilia B.
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CLINICAL_TRIALS trial_result · 2025-08-01Clinical Trial Update: Long-term Safety and Efficacy of Efanesoctocog Alfa (BIVV001) in Previously Treated Patients With Hemophilia A [Phase 3]
Phase 3 study update reporting long-term safety and efficacy of efanesoctocog alfa (BIVV001) in previously treated patients with Hemophilia …
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CLINICAL_TRIALS research · 2025-08-01Clinical Trial Update: Gene Therapy for Chinese Hemophilia A [NA]
A clinical trial update indicates a gene therapy trial for Hemophilia A in China that is currently recruiting.
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CLINICAL_TRIALS research · 2025-08-01Clinical Trial Update: Multidimensional Assessment of Chronic Pain in Severe Haemophilia A
An update on a clinical trial studying multidimensional assessment of chronic pain in adults with severe Hemophilia A without inhibitors, wh…
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CLINICAL_TRIALS research · 2025-08-01Clinical Trial Update: Adult and Adolescent Hemophilia Patients Treated With Marstacimab: a Patient Experience Registry
A patient experience registry study evaluating marstacimab in adult and adolescent patients with hemophilia. The study is currently not recr…
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FDA approval · 2025-07-31FDA Approved: ALHEMO — Supplemental Application (Novo Nordisk)
The FDA document relates to a supplemental application for ALHEMO (concizumab) submitted by Novo Nordisk.
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CLINICAL_TRIALS trial_result · 2025-07-28Clinical Trial Update: A Study of PEGylated Recombinant Factor VIII (BAX855) in Previously Untreated Young Children With Severe Hemophilia A [Phase 3]
A Phase 3 study evaluating PEGylated recombinant Factor VIII (BAX855) in previously untreated young children with severe Hemophilia A has co…
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CLINICAL_TRIALS trial_result · 2025-07-24Clinical Trial Update: A Study to Learn How Safe the Study Treatment BAY94-9027 is and How it Affects the Body in Previously Treated Children Aged 7 to Less Than 12 Years With Severe Hemophilia A, a Genetic Bleeding Disorder That is Caused by the Lack of a Protein Called Clotting Factor 8 (FVIII) in the Blood [Phase 3]
Phase 3 trial assessing the safety and pharmacodynamic effects of BAY94-9027 in previously treated children aged 7 to less than 12 with seve…