Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-10-31Clinical Trial Update: Research Study to Look at How Well the Drug Concizumab Works in Your Body if You Have Haemophilia Without Inhibitors [Phase 3]
Phase 3 trial update evaluating concizumab in people with hemophilia without inhibitors; results have been posted.
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CLINICAL_TRIALS trial_result · 2025-10-24Clinical Trial Update: Nuwiq for Perioperative Management Of Patients With Haemophilia A on Emicizumab Regular Prophylaxis Study [Phase 4]
Phase 4 trial update evaluating Nuwiq (recombinant factor VIII) for perioperative management in patients with Hemophilia A on emicizumab pro…
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CLINICAL_TRIALS trial_result · 2025-10-23Clinical Trial Update: Drug Use Investigation of Kovaltry in Hemophilia A Patients
This document reports the completion of a drug-use investigation evaluating Kovaltry for Hemophilia A.
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CLINICAL_TRIALS research · 2025-10-20Clinical Trial Update: BeCoMe-9: A Clinical Study of BE-101 for the Treatment of Adults With Moderately Severe or Severe Hemophilia B [Phase 1, Phase 2]
Be Biopharma's BE-101 is being studied in Phase 1/2 trials for adults with moderately severe to severe Hemophilia B, and the study is curren…
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CLINICAL_TRIALS research · 2025-10-09Clinical Trial Update: A Study Evaluating Physical Activity and Joint Health in Severe Haemophilia A Patients ≥12 Years Treated Once Weekly With Efanesoctocog Alfa [Phase 3]
Phase 3 study evaluating physical activity and joint health in severe Hemophilia A patients aged 12 and older treated once weekly with efane…
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CLINICAL_TRIALS research · 2025-10-03Clinical Trial Update: High-Altitude Hematology Observation-Stem Cell Transplantation (HALO-SCT)
The document announces a new clinical trial called HALO-SCT, assessing high-altitude observation in stem cell transplantation. It is current…
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CLINICAL_TRIALS research · 2025-10-03Clinical Trial Update: Impact of IV Iron on Bleeding Symptoms in Iron Deficient Patients With Inherited Bleeding Disorders
Clinical trial investigating whether intravenous iron can reduce bleeding symptoms in iron-deficient patients with inherited bleeding disord…
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CLINICAL_TRIALS research · 2025-10-02Clinical Trial Update: A Study to Evaluate Impact of Efanesoctocog Alfa on Long-term Joint Health in Participants With Hemophilia A
This is a clinical trial update for a study evaluating the impact of efanesoctocog alfa on long-term joint health in participants with Hemop…
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CLINICAL_TRIALS research · 2025-10-02Clinical Trial Update: A Study to Evaluate Impact of Efanesoctocog Alfa on Long-term Joint Health in Participants With Hemophilia A in Taiwan
Sanofi is conducting a study to evaluate the impact of efanesoctocog alfa on long-term joint health in participants with Hemophilia A in Tai…
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CLINICAL_TRIALS research · 2025-10-01Clinical Trial Update: The Effects of Virtual Reality-Based Gamified Rehabilitation in Children With Hemophilia [NA]
A clinical trial update for a study on virtual reality-based gamified rehabilitation in children with Hemophilia A, with the study currently…
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CLINICAL_TRIALS trial_result · 2025-09-30Clinical Trial Update: A Study of Recombinant AAV2/6 Human Factor 8 Gene Therapy SB-525 (PF-07055480) in Subjects With Severe Hemophilia A [Phase 2]
Phase 2 study of the recombinant AAV2/6 factor VIII gene therapy SB-525 (PF-07055480) for severe hemophilia A has completed, with results po…
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CLINICAL_TRIALS research · 2025-09-30Clinical Trial Update: A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab [Phase 4]
Phase 4 clinical trial to evaluate Fitusiran for preventing bleeds in people with severe Hemophilia A who previously received Emicizumab; cu…
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CLINICAL_TRIALS trial_result · 2025-09-29Clinical Trial Update: An International Study to Evaluate the Real-world Effectiveness and Usage of Alprolix in Patients With Haemophilia B
This completed international trial evaluated the real-world effectiveness and usage of Alprolix in patients with Hemophilia B.
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EMA approval · 2025-09-25EMA Authorised: Alhemo (concizumab) — Novo Nordisk A/S
EMA authorised Alhemo (concizumab) by Novo Nordisk A/S for the treatment of hemophilia A and hemophilia B.
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CLINICAL_TRIALS research · 2025-09-25Clinical Trial Update: Adverse Event Data Collection From the EUHASS Registry on Turoctocog Alfa Pegol
An ongoing clinical trial update reports adverse event data collection from the EUHASS registry for turoctocog alfa pegol in patients with H…
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CLINICAL_TRIALS research · 2025-09-24Clinical Trial Update: Effects of Emicizumab Treatment in Patients With Hemophilia A
A clinical trial update describes a study evaluating emicizumab treatment in patients with Hemophilia A. The study status is NOT_YET_RECRUIT…
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CLINICAL_TRIALS research · 2025-09-23Clinical Trial Update: Intra-Articular Bevacizumab for Preventing Recurrent Hemarthrosis in Hemophilia With Chronic Synovitis [NA]
A clinical trial is evaluating intra-articular bevacizumab to prevent recurrent joint bleeding (hemarthrosis) in patients with hemophilia an…
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CLINICAL_TRIALS trial_result · 2025-09-18Clinical Trial Update: Pharmacokinetic Assessment of Standard Half-Life (SHL) FVIII, Extended Half-Life (EHL) FVIII, and Efanesoctocog Alfa (BIVV001) in Severe Hemophilia A [Phase 1]
This Phase 1 trial assessed the pharmacokinetics of standard half-life FVIII, extended half-life FVIII, and efanesoctocog alfa (BIVV001) in …
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CLINICAL_TRIALS research · 2025-09-17Clinical Trial Update: Efficacy and Safety of KN057 Prophylaxis in Patients With Haemophilia A or B Without Inhibitors [Phase 3]
A Phase 3 clinical trial evaluating KN057 as prophylaxis for Hemophilia A or Hemophilia B without inhibitors is currently active but not rec…
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CLINICAL_TRIALS trial_result · 2025-09-17Clinical Trial Update: Efficacy and Safety of KN057 Prophylaxis in Patients With Haemophilia A or B With Inhibitors [Phase 3]
Phase 3 clinical trial update on KN057 for prophylaxis in patients with Hemophilia A or B with inhibitors; the study is currently active but…
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CLINICAL_TRIALS research · 2025-09-16Clinical Trial Update: The European Paediatric Network for Haemophilia Management ( PedNet Registry)
Clinical trial update for the European Paediatric Network for Haemophilia Management (PedNet Registry) focusing on pediatric haemophilia car…
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CLINICAL_TRIALS trial_result · 2025-09-11Clinical Trial Update: A Study of BAX 888 in Male Adults With Severe Hemophilia A [Phase 1, Phase 2]
Results from a Phase 1/2 study of BAX 888 in male adults with severe Hemophilia A have been posted.
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EMA approval · 2025-09-10EMA Authorised: Hemlibra (emicizumab) — Roche Registration Limited
The EMA authorised Hemlibra (emicizumab) for Hemophilia A with Roche Registration Limited as the marketing authorization holder, decision da…
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CLINICAL_TRIALS trial_result · 2025-09-10Clinical Trial Update: Comparison of Pulmonary Function, Exercise Capacity, and Physical Activity Level Between Children With Hemophilia and Healthy Controls
This clinical trial update compares pulmonary function, exercise capacity, and physical activity level between children with hemophilia and …
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CLINICAL_TRIALS trial_result · 2025-09-08Clinical Trial Update: Real World Use of Emicizumab in Infants and Children Ages 0-3 Years With Hemophilia A
A completed observational study evaluating real-world use of emicizumab in infants and young children aged 0-3 years with Hemophilia A, repo…