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CLINICAL_TRIALS trial_result · 2025-08-08

Clinical Trial Update: Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B [Phase 3]

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Summary

Phase 3 trial status update for Fitusiran prophylaxis in male pediatric patients aged 1 to less than 12 years with Hemophilia A or B; the study is currently ACT…

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Diseases / indications

Drugs mentioned

  • Fitusiran (fitusiran)

Snippet

Sponsor: Genzyme, a Sanofi Company | Conditions: Hemophilia | Phase 3 | Status: ACTIVE_NOT_RECRUITING