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CLINICAL_TRIALS trial_result · 2026-01-12

Clinical Trial Update: A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)

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Summary

Long-term follow-up study in severe Hemophilia A patients who previously received BMN 270; enrollment is by invitation.

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Diseases / indications

Drugs mentioned

  • BMN 270

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Hemophilia A | Status: ENROLLING_BY_INVITATION