CLINICAL_TRIALS
trial_result
· 2024-11-29
Clinical Trial Update: Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A
Summary
This update summarizes long-term safety and efficacy data from Spark Therapeutics–sponsored gene therapies studied in males with Hemophilia A.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Spark Therapeutics, Inc. | Conditions: Hemophilia A | Status: ACTIVE_NOT_RECRUITING