Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2024-11-29

Clinical Trial Update: Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A

View source ↗

Summary

This update summarizes long-term safety and efficacy data from Spark Therapeutics–sponsored gene therapies studied in males with Hemophilia A.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Spark-sponsored Hemophilia A gene therapies

Snippet

Sponsor: Spark Therapeutics, Inc. | Conditions: Hemophilia A | Status: ACTIVE_NOT_RECRUITING