Friedreich Ataxia
📧 Sign up to get email alerts when something new happens for Friedreich Ataxia.
Sign up freeTop drugs studied for this disease
-
FDA approval · 2023-02-28FDA Approved: SKYCLARYS — Original Application (Biogen)
FDA approved SKYCLARYS (omaveloxolone) from Biogen under Original Application NDA216718 for the treatment of Friedreich's ataxia.
-
CLINICAL_TRIALS trial_result · 2022-11-29Clinical Trial Update: A Study to Learn About the Effects and Safety of RTA 408 (Omaveloxolone) in People Aged 16 to 40 With Friedreich's Ataxia [Phase 2]
Phase 2 trial evaluating the safety and effects of Omaveloxolone (RTA 408) in youths and adults aged 16 to 40 with Friedreich's Ataxia has c…
-
CLINICAL_TRIALS trial_result · 2022-10-13Clinical Trial Update: A Clinical Study to Evaluate the Effect of MIN-102 on the Progression of Friedreich's Ataxia in Male and Female Patients [Phase 2]
Phase 2 clinical trial evaluating MIN-102 for progression in Friedreich's Ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2022-05-27Clinical Trial Update: A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's Ataxia [Phase 3]
Phase 3 trial assessing efficacy, long-term safety, and tolerability of RT001 in Friedreich's Ataxia has completed with results posted.
-
CLINICAL_TRIALS trial_result · 2020-11-27Clinical Trial Update: A First in Human Study of RT001 in Patients With Friedreich's Ataxia [Phase 1, Phase 2]
First-in-human study of RT001 in Friedreich's Ataxia completed; results posted.
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2020-08-31Clinical Trial Update: Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia [Phase 2]
Phase 2 trial update on safety and efficacy of EPI-743 in Friedreich's Ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2020-02-26Clinical Trial Update: Open Trail of γIFN for Friedreich Ataxia [Phase 2]
Phase 2 clinical trial update of gamma-interferon for Friedreich ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2019-12-19Clinical Trial Update: Efficacy, Tolerability, and Pharmacokinetics of Multiple Doses of Oral TAK-831 in Adults With Friedreich Ataxia [Phase 2]
Phase 2 trial updates on multiple-dose oral TAK-831 in adults with Friedreich Ataxia, reporting efficacy, tolerability, and pharmacokinetics…
-
CLINICAL_TRIALS trial_result · 2019-12-05Clinical Trial Update: (+) Epicatechin to Treat Friedreich's Ataxia [Phase 2]
Phase 2 trial investigating epicatechin for Friedreich's ataxia has completed with results posted.
-
CLINICAL_TRIALS trial_result · 2019-06-28Clinical Trial Update: Rehabilitative Trial With Cerebello-Spinal tDCS in Neurodegenerative Ataxia [NA]
Clinical trial update for a rehabilitative tDCS approach in various cerebellar ataxias, status completed with results posted in 2019.
-
CLINICAL_TRIALS trial_result · 2019-03-18Clinical Trial Update: Idebenone to Treat Friedreich's Ataxia [Phase 2]
Phase 2 clinical trial update for idebenone in Friedreich's ataxia is completed.
-
CLINICAL_TRIALS trial_result · 2018-05-18Clinical Trial Update: Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia Study [Phase 3]
Phase 3 trial update evaluating safety, tolerability and efficacy of ACTIMMUNE (interferon gamma-1b) in Friedreich's Ataxia; results posted …
-
CLINICAL_TRIALS trial_result · 2018-05-01Clinical Trial Update: Long-Term Safety Extension Study of ACTIMMUNE® (Interferon γ-1b) in Children and Young Adults With Friedreich's Ataxia [Phase 3]
Long-term safety data from a safety-extension study of interferon gamma-1b (ACTIMMUNE) in children and young adults with Friedreich's Ataxia…
-
CLINICAL_TRIALS trial_result · 2018-03-05Clinical Trial Update: Long-Term Safety and Tolerability of Idebenone in Friedreich's Ataxia Patients (MICONOS Extension) [Phase 3]
The document reports long-term safety and tolerability data from the Phase 3 extension study (MICONOS Extension) of idebenone in Friedreich'…
-
CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia [Phase 3]
Phase 3 study evaluating dose escalation of ACTIMMUNE for Friedreich's Ataxia reported safety, tolerability, and efficacy results; the trial…
-
CLINICAL_TRIALS trial_result · 2017-07-02Clinical Trial Update: Effect of Nicotinamide in Friedreich's Ataxia [Phase 2]
Nicotinamide is being studied in a Phase 2 trial for Friedreich's ataxia, with the trial status listed as unknown.
-
CLINICAL_TRIALS trial_result · 2017-04-21Clinical Trial Update: A Phase IIa Trial to Test Safety and Efficacy Interferon Gamma Treatment in Elevating Frataxin Levels in FRDA Patients [Phase 2]
A Phase IIa trial evaluating whether interferon gamma-1b can safely elevate frataxin levels in Friedreich's ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2016-11-08Clinical Trial Update: Safety Study of Carbamylated Erythropoietin to Treat Patients With the Neurodegenerative Disorder Friedreich's Ataxia [Phase 2]
A Phase 2 safety study of carbamylated erythropoietin in patients with Friedreich's ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2016-10-06Clinical Trial Update: Safety and Pharmacology Study of VP 20629 in Adults With Friedreich's Ataxia [Phase 1]
Phase 1 safety and pharmacology study of VP 20629 in adults with Friedreich's Ataxia has been completed with results posted.
-
CLINICAL_TRIALS trial_result · 2016-09-19Clinical Trial Update: An Objective Double-blind Evaluation of Bupropion and Citalopram in an Individual With Friedreich Ataxia [Phase 4]
A Phase 4, double-blind evaluation of bupropion and citalopram was conducted in a single patient with Friedreich ataxia, with results posted…
-
CLINICAL_TRIALS trial_result · 2016-06-29Clinical Trial Update: EPI-743 in Friedreich's Ataxia Point Mutations [Phase 2]
Phase 2 trial of EPI-743 for Friedreich's Ataxia with point mutations has completed.
-
CLINICAL_TRIALS trial_result · 2016-06-27Clinical Trial Update: A Study of Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia (FRDA) Patients [Phase 3]
Phase 3 study assessing the efficacy, safety and tolerability of idebenone in Friedreich's ataxia has completed, with results posted in 2016…
-
CLINICAL_TRIALS research · 2016-04-12Clinical Trial Update: An Open-label Study of the Effects of Acetyl-L-Carnitine on Cardiovascular Outcomes in Friedreich's Ataxia [NA]
An open-label clinical trial is evaluating the effects of acetyl-L-carnitine on cardiovascular outcomes in Friedreich's Ataxia. The document…
-
CLINICAL_TRIALS trial_result · 2016-03-09Clinical Trial Update: Patient Reported Outcomes in Friedreich's Ataxia Patients After Withdrawal From Treatment With Idebenone (PROTI) [Phase 3]
This Phase 3 trial update summarizes patient-reported outcomes in Friedreich's Ataxia patients after withdrawal from idebenone treatment. Th…
-
CLINICAL_TRIALS trial_result · 2015-08-11Clinical Trial Update: Efficacy Study of Epoetin Alfa in Friedreich Ataxia [Phase 2]
Phase 2 efficacy study evaluating epoetin alfa in Friedreich Ataxia has completed.