Friedreich Ataxia
📧 Sign up to get email alerts when something new happens for Friedreich Ataxia.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-04-08Clinical Trial Update: A Study to Assess the Efficacy and Safety of Vatiquinone for the Treatment of Participants With Friedreich Ataxia [Phase 2, Phase 3]
A Phase 2/3 trial evaluating vatiquinone for Friedreich Ataxia has completed and posted results. The update confirms results availability as…
-
CLINICAL_TRIALS trial_result · 2026-03-25Clinical Trial Update: FRIEDREICH ATAXIA- STEROIDOGENESIS
A clinical trial investigating Friedreich's Ataxia and steroidogenesis conducted by Istanbul University has completed.
-
CLINICAL_TRIALS trial_result · 2026-03-11Clinical Trial Update: NAD+ and Exercise in FA [NA]
A Friedreich's ataxia trial evaluating NAD+ and exercise has completed and posted results.
-
CLINICAL_TRIALS trial_result · 2026-01-16Clinical Trial Update: Measurement of Frataxin mRNA in Biofluids
This completed clinical trial from the University of Florida assesses measurement of frataxin mRNA levels in biofluids in individuals with F…
-
CLINICAL_TRIALS trial_result · 2025-12-23Clinical Trial Update: Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia [Phase 1, Phase 2]
A Phase 1/Phase 2 clinical trial of a gene therapy for cardiomyopathy associated with Friedreich's ataxia is currently active but not recrui…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2025-12-12Clinical Trial Update: FRDA Investigator Initiated Study (IIS) With Elamipretide [Phase 1, Phase 2]
A Phase 1/Phase 2 investigator-initiated study of Elamipretide for Friedreich Ataxia has completed, with results posted on 2025-12-12.
-
CLINICAL_TRIALS trial_result · 2025-11-03Clinical Trial Update: Respiratory Training in Friedreich's Ataxia [NA]
A clinical trial evaluating respiratory training for Friedreich's Ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2025-10-30Clinical Trial Update: A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia [Phase 3]
Phase 3 study of Vatiquinone in Friedreich Ataxia is currently active but not recruiting.
-
CLINICAL_TRIALS trial_result · 2025-08-22Clinical Trial Update: A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxia [Phase 2]
This clinical trial update reports the completion of a Phase 2 study of Vatiquinone for Friedreich's ataxia.
-
CLINICAL_TRIALS trial_result · 2025-02-21Clinical Trial Update: A Single Ascending Dose Study of DT-216P2 in Normal Healthy Participants [Phase 1]
A Phase 1 single ascending dose study of DT-216P2 in healthy participants with Friedreich Ataxia as the target condition; the trial is not y…
-
CLINICAL_TRIALS trial_result · 2025-02-05Clinical Trial Update: Home Based Tele-exercise for People With Chronic Neurological Impairments [NA]
A clinical trial (NCT04564495) evaluating home-based tele-exercise for people with chronic neurological impairments is currently active but …
-
CLINICAL_TRIALS trial_result · 2025-01-16Clinical Trial Update: Neurology Measures in FA Children
This update reports the completion of a clinical trial evaluating neurology measures in children with Friedreich Ataxia and the posting of r…
-
CLINICAL_TRIALS trial_result · 2024-12-04Clinical Trial Update: Safety and Efficacy of Etravirine in Friedreich Ataxia Patients [Phase 2]
Phase 2 clinical trial evaluating the safety and efficacy of etravirine in Friedreich ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2024-11-29Clinical Trial Update: A Double-Blind, Placebo-Controlled, Dose Exploration Study of CTI-1601 in Adult Subjects With Friedreich's Ataxia [Phase 2]
The document notes the completion of a Phase 2 double-blind, placebo-controlled dose-exploration trial of CTI-1601 for Friedreich's Ataxia c…
-
CLINICAL_TRIALS trial_result · 2024-08-05Clinical Trial Update: Instrumented Data Exchange for Ataxia Study
This is a completed clinical trial update from the University of Chicago about an instrumented data exchange study for ataxias, encompassing…
-
CLINICAL_TRIALS trial_result · 2024-07-30Clinical Trial Update: Evaluation of the Effect of Artesunate in Friedreich Ataxia (FA) [Phase 1, Phase 2]
The document reports the completion of a Phase 1/2 clinical trial evaluating artesunate for Friedreich Ataxia. The study was conducted by th…
-
CLINICAL_TRIALS trial_result · 2024-05-22Clinical Trial Update: Micronised Resveratrol as a Treatment for Friedreich Ataxia [Phase 2]
A Phase 2 clinical trial evaluating micronised resveratrol as a treatment for Friedreich's ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2023-10-23Clinical Trial Update: Evaluation of the Effects of Calcitriol's in the Neurological Symptoms of Friedreich's Ataxia Patients [Phase 4]
Phase 4 trial evaluating the effects of calcitriol on neurological symptoms in Friedreich ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2023-07-17Clinical Trial Update: NAD+ Precursor Supplementation in Friedreich's Ataxia [Phase 2]
Phase 2 clinical trial of NAD+ precursor supplementation in Friedreich's ataxia has completed with results posted.
-
CLINICAL_TRIALS trial_result · 2022-11-29Clinical Trial Update: A Study to Learn About the Effects and Safety of RTA 408 (Omaveloxolone) in People Aged 16 to 40 With Friedreich's Ataxia [Phase 2]
Phase 2 trial evaluating the safety and effects of Omaveloxolone (RTA 408) in youths and adults aged 16 to 40 with Friedreich's Ataxia has c…
-
CLINICAL_TRIALS trial_result · 2022-10-13Clinical Trial Update: A Clinical Study to Evaluate the Effect of MIN-102 on the Progression of Friedreich's Ataxia in Male and Female Patients [Phase 2]
Phase 2 clinical trial evaluating MIN-102 for progression in Friedreich's Ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2022-05-27Clinical Trial Update: A Study to Assess Efficacy, Long Term Safety and Tolerability of RT001 in Subjects With Friedreich's Ataxia [Phase 3]
Phase 3 trial assessing efficacy, long-term safety, and tolerability of RT001 in Friedreich's Ataxia has completed with results posted.
-
CLINICAL_TRIALS trial_result · 2020-11-27Clinical Trial Update: A First in Human Study of RT001 in Patients With Friedreich's Ataxia [Phase 1, Phase 2]
First-in-human study of RT001 in Friedreich's Ataxia completed; results posted.
-
CLINICAL_TRIALS trial_result · 2020-08-31Clinical Trial Update: Safety and Efficacy of EPI-743 in Patients With Friedreich's Ataxia [Phase 2]
Phase 2 trial update on safety and efficacy of EPI-743 in Friedreich's Ataxia has completed.
-
CLINICAL_TRIALS trial_result · 2020-02-26Clinical Trial Update: Open Trail of γIFN for Friedreich Ataxia [Phase 2]
Phase 2 clinical trial update of gamma-interferon for Friedreich ataxia has completed.