Friedreich Ataxia
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CLINICAL_TRIALS trial_result · 2025-08-22Clinical Trial Update: A Study of Vatiquinone for the Treatment of Participants With Friedreich Ataxia [Phase 2]
This clinical trial update reports the completion of a Phase 2 study of Vatiquinone for Friedreich's ataxia.
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CLINICAL_TRIALS research · 2025-08-19Clinical Trial Update: Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA)
Clinical trial update describing a study to characterize the cardiac phenotype in Friedreich's Ataxia, sponsored by Weill Medical College of…
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CLINICAL_TRIALS research · 2025-07-31Clinical Trial Update: Electroencephalogram in Patients With Friedreich's Ataxia for the Study of the Structural and Functional Connectome. [NA]
This clinical trial update shows that recruitment is ongoing for a study using electroencephalography to assess the structural and functiona…
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CLINICAL_TRIALS research · 2025-06-26Clinical Trial Update: A Study to Learn How BIIB141 (Omaveloxolone) Affects the Health of Participants With Friedrich's Ataxia Who Took it During Pregnancy and/or During Breastfeeding and About the Health of Their Babies
A clinical trial is assessing the effects of BIIB141 (omaveloxolone) in people with Friedreich ataxia who took it during pregnancy or breast…
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CLINICAL_TRIALS research · 2025-06-17Clinical Trial Update: Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
This is a clinical trial update for the Friedreich Ataxia Global Clinical Consortium Unified Natural History Study, a natural history study …
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CLINICAL_TRIALS research · 2025-06-10Clinical Trial Update: Efficacy of Omaveloxolone Treatment for Dysphagia in French Patients With Friedreich's Ataxia
Clinical trial update indicating a study of omaveloxolone for dysphagia in French patients with Friedreich's ataxia, which is currently not …
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CLINICAL_TRIALS withdrawal · 2025-06-08Clinical Trial Update: Understanding the Natural History Early in the Course or Presentation of Friedreich Ataxia
The clinical trial NCT06560346, sponsored by Friedreich's Ataxia Research Alliance, has been withdrawn; it previously sought to understand t…
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CLINICAL_TRIALS research · 2025-05-18Clinical Trial Update: A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's Ataxia [Phase 1, Phase 2]
Design Therapeutics is conducting a multiple ascending dose study of DT-216P2 in patients with Friedreich's ataxia. The trial is a Phase 1/2…
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CLINICAL_TRIALS research · 2025-05-07Clinical Trial Update: Characterisation of the Cognitive Profile of Patients Suffering From Friedreich's Ataxia
This clinical trial study aims to characterize the cognitive profile of patients with Friedreich's ataxia and is currently recruiting.
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CLINICAL_TRIALS research · 2025-05-02Clinical Trial Update: Efficacy of Stabilometric Platform to Improve Standing Balance in Patients With Friedreich's Ataxia [NA]
This clinical trial update notes ongoing recruitment for a study evaluating whether a stabilometric platform can improve standing balance in…
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CLINICAL_TRIALS research · 2025-04-10Clinical Trial Update: A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors
Biogen is conducting an ongoing long-term safety study of omaveloxolone (BIIB141) in Friedreich's Ataxia patients who are being treated with…
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CLINICAL_TRIALS trial_result · 2025-02-21Clinical Trial Update: A Single Ascending Dose Study of DT-216P2 in Normal Healthy Participants [Phase 1]
A Phase 1 single ascending dose study of DT-216P2 in healthy participants with Friedreich Ataxia as the target condition; the trial is not y…
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CLINICAL_TRIALS trial_result · 2025-02-05Clinical Trial Update: Home Based Tele-exercise for People With Chronic Neurological Impairments [NA]
A clinical trial (NCT04564495) evaluating home-based tele-exercise for people with chronic neurological impairments is currently active but …
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CLINICAL_TRIALS trial_result · 2025-01-16Clinical Trial Update: Neurology Measures in FA Children
This update reports the completion of a clinical trial evaluating neurology measures in children with Friedreich Ataxia and the posting of r…
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FDA approval · 2024-12-20FDA Approved: SKYCLARYS — Supplemental Application (Biogen)
The FDA approved a supplemental application for SKYCLARYS (omaveloxolone) submitted by Biogen.
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CLINICAL_TRIALS trial_result · 2024-12-04Clinical Trial Update: Safety and Efficacy of Etravirine in Friedreich Ataxia Patients [Phase 2]
Phase 2 clinical trial evaluating the safety and efficacy of etravirine in Friedreich ataxia has completed.
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CLINICAL_TRIALS trial_result · 2024-11-29Clinical Trial Update: A Double-Blind, Placebo-Controlled, Dose Exploration Study of CTI-1601 in Adult Subjects With Friedreich's Ataxia [Phase 2]
The document notes the completion of a Phase 2 double-blind, placebo-controlled dose-exploration trial of CTI-1601 for Friedreich's Ataxia c…
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CLINICAL_TRIALS research · 2024-11-27Clinical Trial Update: A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals with Friedreich Ataxia (TRACK-FA)
This is an observational natural history study designed to track brain and spinal cord changes in individuals with Friedreich Ataxia. The st…
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CLINICAL_TRIALS research · 2024-10-04Clinical Trial Update: FA Clinical Outcome Measures
Friedreich's ataxia researchers have provided an update on clinical outcome measures for trial NCT03090789. The study is currently active bu…
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CLINICAL_TRIALS trial_result · 2024-08-05Clinical Trial Update: Instrumented Data Exchange for Ataxia Study
This is a completed clinical trial update from the University of Chicago about an instrumented data exchange study for ataxias, encompassing…
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CLINICAL_TRIALS trial_result · 2024-07-30Clinical Trial Update: Evaluation of the Effect of Artesunate in Friedreich Ataxia (FA) [Phase 1, Phase 2]
The document reports the completion of a Phase 1/2 clinical trial evaluating artesunate for Friedreich Ataxia. The study was conducted by th…
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CLINICAL_TRIALS trial_result · 2024-05-22Clinical Trial Update: Micronised Resveratrol as a Treatment for Friedreich Ataxia [Phase 2]
A Phase 2 clinical trial evaluating micronised resveratrol as a treatment for Friedreich's ataxia has completed.
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FDA approval · 2024-01-25FDA Approved: SKYCLARYS — Supplemental Application (Biogen)
FDA approved Biogen's supplemental application for SKYCLARYS (omaveloxolone).
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CLINICAL_TRIALS trial_result · 2023-10-23Clinical Trial Update: Evaluation of the Effects of Calcitriol's in the Neurological Symptoms of Friedreich's Ataxia Patients [Phase 4]
Phase 4 trial evaluating the effects of calcitriol on neurological symptoms in Friedreich ataxia has completed.
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CLINICAL_TRIALS trial_result · 2023-07-17Clinical Trial Update: NAD+ Precursor Supplementation in Friedreich's Ataxia [Phase 2]
Phase 2 clinical trial of NAD+ precursor supplementation in Friedreich's ataxia has completed with results posted.