Friedreich Ataxia
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: Clinical Course Of Disease In Participants With FA-CM
The clinical trial NCT06865482 by Lexeo Therapeutics is currently recruiting to study the clinical course of disease in Friedreich ataxia wi…
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CLINICAL_TRIALS research · 2026-04-02Clinical Trial Update: Friedreich Ataxia Nerve Ultrasund
A clinical trial evaluating nerve ultrasound as a biomarker in Friedreich ataxia is currently recruiting. Sponsored by Centre Hospitalier Un…
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CLINICAL_TRIALS research · 2026-04-01Clinical Trial Update: Patient-reported, Health Economic and Psychosocial Outcomes in Friedreich Ataxia
This clinical trial update outlines an ongoing study by DZNE evaluating patient-reported outcomes, health economic considerations, and psych…
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CLINICAL_TRIALS research · 2026-03-31Clinical Trial Update: Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia [Phase 1]
This clinical trial update reports a Phase 1a/1b study of AAVrh.10hFXN gene therapy for Friedreich's ataxia-related cardiomyopathy, currentl…
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CLINICAL_TRIALS research · 2026-03-24Clinical Trial Update: An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia [Phase 2]
An open-label Phase 2 clinical trial evaluating CTI-1601 in Friedreich's ataxia is currently recruiting.
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CLINICAL_TRIALS research · 2026-03-16Clinical Trial Update: A Study to Learn More About the Effects and Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Aged 2 to 15 Years Old (BRAVE) [Phase 3]
The BRAVE Phase 3 trial is recruiting to evaluate omaveloxolone (BIIB141) for Friedreich's ataxia in children aged 2 to 15 and assess long-t…
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CLINICAL_TRIALS research · 2026-03-09Clinical Trial Update: A Study of SGT-212 Gene Therapy in Friedreich's Ataxia [Phase 1]
A Phase 1 study of SGT-212 gene therapy for Friedreich's ataxia is currently recruiting.
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CLINICAL_TRIALS research · 2026-03-02Clinical Trial Update: Cardiac Output and Fatigue in Friedreich's Ataxia [NA]
Clinical trial update examining cardiac output and fatigue in Friedreich's Ataxia. The study is currently NOT_YET_RECRUITING.
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CLINICAL_TRIALS research · 2026-01-07Clinical Trial Update: A Study to Find Out How BIIB141 (Omaveloxolone) is Processed in the Body and to Learn More About Its Safety in Participants With Friedreich's Ataxia Aged 2 to 15 Years Old [Phase 1]
Phase 1 study to assess how BIIB141 (Omaveloxolone) is processed in the body and its safety in children ages 2 to 15 with Friedreich's Ataxi…
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CLINICAL_TRIALS research · 2025-10-03Clinical Trial Update: Patient Registry of the European Friedreich's Ataxia Consortium for Translational Studies (EFACTS)
Update on the European Friedreich's Ataxia Consortium for Translational Studies (EFACTS) patient registry, noting that the study status is C…
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CLINICAL_TRIALS research · 2025-09-23Clinical Trial Update: Biomarkers in Friedreich's Ataxia
A University of Florida-sponsored clinical trial is currently recruiting to study biomarkers in Friedreich's Ataxia.
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CLINICAL_TRIALS research · 2025-08-19Clinical Trial Update: Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA)
Clinical trial update describing a study to characterize the cardiac phenotype in Friedreich's Ataxia, sponsored by Weill Medical College of…
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CLINICAL_TRIALS research · 2025-07-31Clinical Trial Update: Electroencephalogram in Patients With Friedreich's Ataxia for the Study of the Structural and Functional Connectome. [NA]
This clinical trial update shows that recruitment is ongoing for a study using electroencephalography to assess the structural and functiona…
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CLINICAL_TRIALS research · 2025-06-26Clinical Trial Update: A Study to Learn How BIIB141 (Omaveloxolone) Affects the Health of Participants With Friedrich's Ataxia Who Took it During Pregnancy and/or During Breastfeeding and About the Health of Their Babies
A clinical trial is assessing the effects of BIIB141 (omaveloxolone) in people with Friedreich ataxia who took it during pregnancy or breast…
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CLINICAL_TRIALS research · 2025-06-17Clinical Trial Update: Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
This is a clinical trial update for the Friedreich Ataxia Global Clinical Consortium Unified Natural History Study, a natural history study …
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CLINICAL_TRIALS research · 2025-06-10Clinical Trial Update: Efficacy of Omaveloxolone Treatment for Dysphagia in French Patients With Friedreich's Ataxia
Clinical trial update indicating a study of omaveloxolone for dysphagia in French patients with Friedreich's ataxia, which is currently not …
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CLINICAL_TRIALS research · 2025-05-18Clinical Trial Update: A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's Ataxia [Phase 1, Phase 2]
Design Therapeutics is conducting a multiple ascending dose study of DT-216P2 in patients with Friedreich's ataxia. The trial is a Phase 1/2…
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CLINICAL_TRIALS research · 2025-05-07Clinical Trial Update: Characterisation of the Cognitive Profile of Patients Suffering From Friedreich's Ataxia
This clinical trial study aims to characterize the cognitive profile of patients with Friedreich's ataxia and is currently recruiting.
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CLINICAL_TRIALS research · 2025-05-02Clinical Trial Update: Efficacy of Stabilometric Platform to Improve Standing Balance in Patients With Friedreich's Ataxia [NA]
This clinical trial update notes ongoing recruitment for a study evaluating whether a stabilometric platform can improve standing balance in…
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CLINICAL_TRIALS research · 2025-04-10Clinical Trial Update: A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors
Biogen is conducting an ongoing long-term safety study of omaveloxolone (BIIB141) in Friedreich's Ataxia patients who are being treated with…
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CLINICAL_TRIALS research · 2024-11-27Clinical Trial Update: A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals with Friedreich Ataxia (TRACK-FA)
This is an observational natural history study designed to track brain and spinal cord changes in individuals with Friedreich Ataxia. The st…
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CLINICAL_TRIALS research · 2024-10-04Clinical Trial Update: FA Clinical Outcome Measures
Friedreich's ataxia researchers have provided an update on clinical outcome measures for trial NCT03090789. The study is currently active bu…
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CLINICAL_TRIALS research · 2016-04-12Clinical Trial Update: An Open-label Study of the Effects of Acetyl-L-Carnitine on Cardiovascular Outcomes in Friedreich's Ataxia [NA]
An open-label clinical trial is evaluating the effects of acetyl-L-carnitine on cardiovascular outcomes in Friedreich's Ataxia. The document…
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CLINICAL_TRIALS research · 2006-07-12Clinical Trial Update: Safety Study of Idebenone to Treat Friedreich's Ataxia [Phase 1]
Notes completion of a Phase 1 safety study evaluating idebenone for Friedreich's ataxia.