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CLINICAL_TRIALS research · 2026-03-09

Clinical Trial Update: A Study of SGT-212 Gene Therapy in Friedreich's Ataxia [Phase 1]

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Summary

A Phase 1 study of SGT-212 gene therapy for Friedreich's ataxia is currently recruiting.

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Diseases / indications

Drugs mentioned

  • SGT-212

Snippet

Sponsor: Solid Biosciences Inc. | Conditions: Friedreich's Ataxia (FA) | Phase 1 | Status: RECRUITING