Clinical Trial Update: Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia [Phase 1]

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Summary

This clinical trial update reports a Phase 1a/1b study of AAVrh.10hFXN gene therapy for Friedreich's ataxia-related cardiomyopathy, currently recruiting.

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Diseases / indications

• Cardiac Hypertrophy
• Cardiomyopathy
• Friedreich Ataxia
• Myocardial Fibrosis

Drugs mentioned

• AAVrh.10hFXN gene therapy

Snippet

Sponsor: Weill Medical College of Cornell University | Conditions: Friedreich Ataxia, Cardiomyopathies | Phase 1 | Status: RECRUITING