CLINICAL_TRIALS
research
· 2025-12-22
Clinical Trial Update: Gene Therapy for Fanconi Anemia, Complementation Group A [Phase 2]
Summary
This entry reports a Phase 2 gene therapy trial for Fanconi anemia, complementation group A, which is currently active but not recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Rocket Pharmaceuticals Inc. | Conditions: Fanconi Anemia Complementation Group A | Phase 2 | Status: ACTIVE_NOT_RECRUITING