Canavan Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-17Clinical Trial Update: A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial) [Phase 1, Phase 2]
CANaspire study is evaluating an AAV9-mediated gene therapy for Canavan disease and is currently recruiting in Phase 1/2.
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CLINICAL_TRIALS research · 2025-11-14Clinical Trial Update: rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease [Phase 1, Phase 2]
This clinical trial update outlines Phase 1/2 testing of rAAV-Olig001-ASPA gene therapy for Canavan disease. Enrollment is by invitation.
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CLINICAL_TRIALS research · 2025-10-23Clinical Trial Update: The Myelin Disorders Biorepository Project
This clinical trials update describes the Myelin Disorders Biorepository Project (NCT03047369) from Children’s Hospital of Philadelphia, cur…
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CLINICAL_TRIALS research · 2006-08-15Clinical Trial Update: GTA-Glyceryltriacetate for Canavan Disease [Phase 1]
Phase 1 clinical trial update for GTA-Glyceryltriacetate in Canavan disease; the trial status is currently unknown.