CLINICAL_TRIALS
research
· 2026-04-17
Clinical Trial Update: A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial) [Phase 1, Phase 2]
Summary
CANaspire study is evaluating an AAV9-mediated gene therapy for Canavan disease and is currently recruiting in Phase 1/2.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Aspa Therapeutics | Conditions: Canavan Disease | Phase 1, Phase 2 | Status: RECRUITING