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CLINICAL_TRIALS research · 2026-04-17

Clinical Trial Update: A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial) [Phase 1, Phase 2]

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Summary

CANaspire study is evaluating an AAV9-mediated gene therapy for Canavan disease and is currently recruiting in Phase 1/2.

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Diseases / indications

Drugs mentioned

  • AAV9 gene therapy for Canavan disease

Snippet

Sponsor: Aspa Therapeutics | Conditions: Canavan Disease | Phase 1, Phase 2 | Status: RECRUITING