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CLINICAL_TRIALS research · 2025-11-14

Clinical Trial Update: rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease [Phase 1, Phase 2]

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Summary

This clinical trial update outlines Phase 1/2 testing of rAAV-Olig001-ASPA gene therapy for Canavan disease. Enrollment is by invitation.

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Diseases / indications

Drugs mentioned

  • rAAV-Olig001-ASPA Gene Therapy

Snippet

Sponsor: Myrtelle Inc. | Conditions: Canavan Disease | Phase 1, Phase 2 | Status: ENROLLING_BY_INVITATION