CLINICAL_TRIALS
research
· 2025-11-14
Clinical Trial Update: rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease [Phase 1, Phase 2]
Summary
This clinical trial update outlines Phase 1/2 testing of rAAV-Olig001-ASPA gene therapy for Canavan disease. Enrollment is by invitation.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Myrtelle Inc. | Conditions: Canavan Disease | Phase 1, Phase 2 | Status: ENROLLING_BY_INVITATION