Alpha-thalassemia
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Screening for Alpha Thalassemia in Healthy Volunteers
Clinical trial update indicating alpha thalassemia screening in healthy volunteers; the study is currently active but not recruiting.
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants
NIAID-sponsored clinical trial update indicates recruitment is ongoing to collect human biospecimens for basic and clinical research into gl…
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CLINICAL_TRIALS research · 2026-04-08Clinical Trial Update: A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) [Phase 3]
A Phase 3 pediatric study evaluating mitapivat for transfusion-dependent alpha- and beta-thalassemia to assess efficacy, pharmacokinetics, a…
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CLINICAL_TRIALS research · 2026-04-08Clinical Trial Update: A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia [Phase 3]
This clinical trial update describes a Phase 3 study to evaluate the efficacy, pharmacokinetics, and safety of mitapivat in pediatric partic…
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CLINICAL_TRIALS trial_result · 2026-03-24Clinical Trial Update: A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia [Phase 2]
Phase 2 study to assess the efficacy and safety of luspatercept in adults with alpha-thalassemia, with safety and pharmacokinetics in adoles…
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CLINICAL_TRIALS trial_result · 2025-05-25Clinical Trial Update: A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) [Phase 3]
Phase 3 trial evaluating the efficacy and safety of mitapivat in transfusion-dependent alpha- and beta-thalassemia; results have been posted…
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CLINICAL_TRIALS research · 2025-04-04Clinical Trial Update: International Registry of Patients With Alpha Thalassemia
University of California, San Francisco is sponsoring an international registry (NCT04872179) to collect data from patients with alpha-thala…
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CLINICAL_TRIALS research · 2024-11-14Clinical Trial Update: FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases
FLOWER is a longitudinal epidemiology study by xCures to follow outcomes across multiple rare diseases, and the study is currently recruitin…
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CLINICAL_TRIALS research · 2024-09-19Clinical Trial Update: Genetic Profile of Alpha Thalassemia Children at Sohag University Hospital .
Clinical trial investigating the genetic profile of Alpha-thalassemia in children at Sohag University Hospital; currently recruiting.
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CLINICAL_TRIALS research · 2024-06-03Clinical Trial Update: Safety and Efficacy of RM-004 Cells for Hemoglobin H-Constant Spring Disease [EARLY_Phase 1]
An early Phase 1 trial evaluating the safety and potential efficacy of RM-004 cell therapy for Alpha-thalassemia with Hemoglobin H disease d…
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CLINICAL_TRIALS trial_result · 2017-08-10Clinical Trial Update: Genetics of Alpha Thalassemia in Israeli Ethnic Groups
This clinical trial update summarizes a completed study on the genetics of alpha-thalassemia across Israeli ethnic groups.
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CLINICAL_TRIALS trial_result · 2015-09-01Clinical Trial Update: Demographic, Clinical and Laboratory Characteristics of Children With Alpha Thalassemia in Northern Israel
This completed clinical trial reports demographic, clinical, and laboratory characteristics of children with alpha-thalassemia in Northern I…
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CLINICAL_TRIALS trial_result · 2015-06-02Clinical Trial Update: Use of 3D/4D Ultrasound in the Evaluation of Fetal Anomalies
This clinical trial update notes the completion of a study assessing the use of 3D/4D ultrasound to evaluate fetal anomalies in pregnancies …