Clinical Trial Update: A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia [Phase 3]

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Summary

This clinical trial update describes a Phase 3 study to evaluate the efficacy, pharmacokinetics, and safety of mitapivat in pediatric participants with non-tran…

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Diseases / indications

• Alpha-thalassemia
• Beta-thalassemia

Drugs mentioned

• Pyrukynd (mitapivat)

Snippet

Sponsor: Agios Pharmaceuticals, Inc. | Conditions: Non-Transfusion-dependent Alpha-Thalassemia, Non-Transfusion-dependent Beta-Thalassemia | Phase 3 | Status: NOT_YET_RECRUITING