Clinical Trial Update: A Study to Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) [Phase 3]

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Summary

A Phase 3 pediatric study evaluating mitapivat for transfusion-dependent alpha- and beta-thalassemia to assess efficacy, pharmacokinetics, and safety; the trial…

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Diseases / indications

• Alpha-thalassemia
• Beta-thalassemia

Drugs mentioned

• Mitapivat (mitapivat)

Snippet

Sponsor: Agios Pharmaceuticals, Inc. | Conditions: Transfusion-dependent Alpha-Thalassemia, Transfusion-dependent Beta-Thalassemia | Phase 3 | Status: NOT_YET_RECRUITING