Alpha-thalassemia

• CLINICAL_TRIALS trial_result · 2026-03-24
  Clinical Trial Update: A Study to Determine the Efficacy and Safety of Luspatercept in Adult Participants and to Evaluate the Safety and Pharmacokinetics in and Adolescent Participants With Alpha (α)-Thalassemia [Phase 2]

  Phase 2 study to assess the efficacy and safety of luspatercept in adults with alpha-thalassemia, with safety and pharmacokinetics in adoles…

• CLINICAL_TRIALS trial_result · 2025-05-25
  Clinical Trial Update: A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT) [Phase 3]

  Phase 3 trial evaluating the efficacy and safety of mitapivat in transfusion-dependent alpha- and beta-thalassemia; results have been posted…

• CLINICAL_TRIALS trial_result · 2017-08-10
  Clinical Trial Update: Genetics of Alpha Thalassemia in Israeli Ethnic Groups

  This clinical trial update summarizes a completed study on the genetics of alpha-thalassemia across Israeli ethnic groups.

• CLINICAL_TRIALS trial_result · 2015-09-01
  Clinical Trial Update: Demographic, Clinical and Laboratory Characteristics of Children With Alpha Thalassemia in Northern Israel

  This completed clinical trial reports demographic, clinical, and laboratory characteristics of children with alpha-thalassemia in Northern I…

• CLINICAL_TRIALS trial_result · 2015-06-02
  Clinical Trial Update: Use of 3D/4D Ultrasound in the Evaluation of Fetal Anomalies

  This clinical trial update notes the completion of a study assessing the use of 3D/4D ultrasound to evaluate fetal anomalies in pregnancies …

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