Allan-herndon-dudley Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency
Expanded access program update for tiratricol in patients with Monocarboxylate Transporter 8 deficiency (Allan-Herndon-Dudley Syndrome).
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CLINICAL_TRIALS withdrawal · 2026-04-08Clinical Trial Update: Withdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency) [Phase 3]
A Phase 3 trial evaluating tiratricol for Monocarboxylate Transporter 8 Deficiency has involved withdrawal of tiratricol treatment in male p…
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Triac Trial II in MCT8 Deficiency Patients [Phase 2]
Phase 2 trial (Triac Trial II) evaluating tiratricol for Allan-Herndon-Dudley Syndrome is active but not recruiting.
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CLINICAL_TRIALS research · 2025-12-11Clinical Trial Update: Rescue of Infants With MCT8 Deficiency
The update notes the availability of a clinical trial aimed at rescuing infants with MCT8 deficiency (Allan-Herndon-Dudley syndrome).
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EMA approval · 2024-12-13First treatment for peripheral thyrotoxicosis in patients with Allan-Herndon-Dudley syndrome
The EMA approved Emcitate as the first treatment for peripheral thyrotoxicosis in patients with Allan-Herndon-Dudley syndrome, and it can be…
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CLINICAL_TRIALS research · 2024-08-22Clinical Trial Update: Register for Patients With Thyroid Hormone Resistance.
Charite University, Berlin, is recruiting participants for a clinical trial addressing thyroid hormone resistance, including Allan-Herndon-D…
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CLINICAL_TRIALS trial_result · 2024-04-25Clinical Trial Update: MCT8 Deficiency Caregiver Study
This clinical trial update indicates that the caregiver study for Monocarboxylate Transporter 8 (MCT8) deficiency/Allan-Herndon-Dudley Syndr…
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CLINICAL_TRIALS trial_result · 2019-04-16Clinical Trial Update: Thyroid Hormone Analog Therapy in MCT8 Deficiency: Triac Trial Patients [Phase 2]
Phase 2 trial update for Triac therapy in MCT8 deficiency (Allan-Herndon-Dudley Syndrome) has completed.