Clinical Trial Update: Rescue of Infants With MCT8 Deficiency

View source ↗

Summary

The update notes the availability of a clinical trial aimed at rescuing infants with MCT8 deficiency (Allan-Herndon-Dudley syndrome).

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Allan-herndon-dudley Syndrome

Snippet

Sponsor: Roy E. Weiss, M.D. | Conditions: Mct8 (Slc16A2)-Specific Thyroid Hormone Cell Transporter Deficiency | Status: AVAILABLE