Zellweger Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2020-12-17Clinical Trial Update: Hydroxychloroquine Administration for Reduction of Pexophagy [Phase 2]
Phase 2 clinical trial evaluating hydroxychloroquine to reduce pexophagy in Zellweger syndrome and peroxisome biogenesis disorders has compl…
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CLINICAL_TRIALS trial_result · 2020-07-15Clinical Trial Update: Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid [Phase 3]
Phase 3 trial update on compassionate use of cholic acid for infants with inborn errors of bile acid metabolism; study completed with result…
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CLINICAL_TRIALS trial_result · 2015-03-25Clinical Trial Update: Study of Bile Acids in Patients With Peroxisomal Disorders [NA]
A clinical trial evaluating bile acids for peroxisomal disorders has been terminated, involving diseases such as Infantile Refsum's Disease …