Clinical Trial Update: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis [Phase 2]

View source ↗

Summary

Phase 2 trial update describing allogeneic hematopoietic cell transplantation for metabolic disorders and severe osteopetrosis, with the study currently ACTIVE_…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Alpha-mannosidosis
• Fucosidosis
• Hunter Syndrome
• Hurler Syndrome
• Maroteaux-lamy Syndrome
• Niemann-pick Disease Type
• Osteopetrosis
• Sanfilippo Syndrome Type

Drugs mentioned

• Allogeneic hematopoietic cell transplantation (allo-HCT)

Snippet

Sponsor: Masonic Cancer Center, University of Minnesota | Conditions: Mucopolysaccharidosis Disorders, Hurler Syndrome | Phase 2 | Status: ACTIVE_NOT_RECRUITING