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MT2013-31: Allogeneic Hematopoietic Cell Transplantation for Inherited Metabolic Disorders and Severe Osteopetrosis Following Conditioning With Busulfan (Therapeutic Drug Monitoring), Fludarabine +/- ATG

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT02171104
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:28:41.580218+00:00
Published At
2026-01-07T00:00:00+00:00
Record Updated At
2026-01-07
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Mucopolysaccharidosis Disorders", "Hurler Syndrome", "Hunter Syndrome", "Maroteaux Lamy Syndrome", "Sly Syndrome", "Alpha-Mannosidosis", "Fucosidosis", "Aspartylglucosaminuria", "Glycoprotein Metabolic Disorders", "Sphingolipidoses", "Recessive Leukodystrophies", "Globoid Cell Leukodystrophy", "Metachromatic Leukodystrophy", "Niemann-Pick B", "Niemann-Pick C Subtype 2", "Sphingomyelin Deficiency", "Peroxisomal Disorders", "Adrenoleukodystrophy With Cerebral Involvement", "Zellweger Syndrome", "Neonatal Adrenoleukodystrophy", "Infantile Refsum Disease", "Acyl-CoA Oxidase Deficiency", "D-Bifunctional Enzyme Deficiency", "Multifunctional Enzyme Deficiency", "Alpha-methylacyl-CoA Racmase Deficiency", "Mitochondrial Neurogastrointestingal Encephalopathy", "Severe Osteopetrosis", "Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation)", "Inherited Metabolic Disorders"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2026-01-07"
protocolSection.identificationModule.nctId
"NCT02171104"
protocolSection.identificationModule.officialTitle
"MT2013-31: Allogeneic Hematopoietic Cell Transplantation for Inherited Metabolic Disorders and Severe Osteopetrosis Following Conditioning With Busulfan (Therapeutic Drug Monitoring), Fludarabine +/- ATG"
protocolSection.statusModule.overallStatus
"ACTIVE_NOT_RECRUITING"
protocolSection.designModule.phases
["PHASE2"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • Mucopolysaccharidosis Disorders (protocolSection.conditionsModule.conditions)
  • Hurler Syndrome (protocolSection.conditionsModule.conditions)
  • Hunter Syndrome (protocolSection.conditionsModule.conditions)
  • Maroteaux Lamy Syndrome (protocolSection.conditionsModule.conditions)
  • Sly Syndrome (protocolSection.conditionsModule.conditions)
  • Alpha-Mannosidosis (protocolSection.conditionsModule.conditions)
  • Fucosidosis (protocolSection.conditionsModule.conditions)
  • Aspartylglucosaminuria (protocolSection.conditionsModule.conditions)
  • Glycoprotein Metabolic Disorders (protocolSection.conditionsModule.conditions)
  • Sphingolipidoses (protocolSection.conditionsModule.conditions)
  • Recessive Leukodystrophies (protocolSection.conditionsModule.conditions)
  • Globoid Cell Leukodystrophy (protocolSection.conditionsModule.conditions)
  • Metachromatic Leukodystrophy (protocolSection.conditionsModule.conditions)
  • Niemann-Pick B (protocolSection.conditionsModule.conditions)
  • Niemann-Pick C Subtype 2 (protocolSection.conditionsModule.conditions)
  • Sphingomyelin Deficiency (protocolSection.conditionsModule.conditions)
  • Peroxisomal Disorders (protocolSection.conditionsModule.conditions)
  • Adrenoleukodystrophy With Cerebral Involvement (protocolSection.conditionsModule.conditions)
  • Zellweger Syndrome (protocolSection.conditionsModule.conditions)
  • Neonatal Adrenoleukodystrophy (protocolSection.conditionsModule.conditions)
  • Infantile Refsum Disease (protocolSection.conditionsModule.conditions)
  • Acyl-CoA Oxidase Deficiency (protocolSection.conditionsModule.conditions)
  • D-Bifunctional Enzyme Deficiency (protocolSection.conditionsModule.conditions)
  • Multifunctional Enzyme Deficiency (protocolSection.conditionsModule.conditions)
  • Alpha-methylacyl-CoA Racmase Deficiency (protocolSection.conditionsModule.conditions)
  • Mitochondrial Neurogastrointestingal Encephalopathy (protocolSection.conditionsModule.conditions)
  • Severe Osteopetrosis (protocolSection.conditionsModule.conditions)
  • Hereditary Leukoencephalopathy With Axonal Spheroids (HDLS; CSF1R Mutation) (protocolSection.conditionsModule.conditions)
  • Inherited Metabolic Disorders (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

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