Wolfram Syndrome
📧 Sign up to get email alerts when something new happens for Wolfram Syndrome.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-04-14Clinical Trial Update: AMX0035 in Adult Patients With Wolfram Syndrome [Phase 2]
AMX0035 is being studied in a Phase 2 trial for adult patients with Wolfram syndrome, and the study is currently active but not recruiting.
-
CLINICAL_TRIALS trial_result · 2024-08-06Clinical Trial Update: I-Tracking Neurodegeneration in Early Wolfram Syndrome
The clinical trial NCT03951298 investigating neurodegeneration in early Wolfram Syndrome has completed.
-
CLINICAL_TRIALS trial_result · 2024-07-31Clinical Trial Update: Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome [Phase 2]
Phase 2 study evaluating the efficacy and safety of sodium valproate in pediatric and adult patients with Wolfram syndrome; study is current…
-
CLINICAL_TRIALS trial_result · 2024-03-13Clinical Trial Update: A Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating dantrolene sodium in pediatric and adult Wolfram syndrome patients has completed with results posted.
-
CLINICAL_TRIALS trial_result · 2024-02-22Clinical Trial Update: Tirzepatide Monotherapy in Patients With Wolfram Syndrome Type 1 [Phase 2]
A Phase 2 trial evaluating tirzepatide as monotherapy in patients with Wolfram Syndrome is ongoing, with the status not yet determined.
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2023-11-28Clinical Trial Update: Efficacy Study of Daily Administration of VPA in Patients Affected by Wolfram Syndrome [Phase 2]
Phase 2 trial update evaluating daily valproic acid (VPA) efficacy in patients with Wolfram Syndrome; status not disclosed.
-
CLINICAL_TRIALS trial_result · 2018-07-11Clinical Trial Update: Tracking Neurodegeneration in Early Wolfram Syndrome
The clinical trial 'Tracking Neurodegeneration in Early Wolfram Syndrome' (NCT02455414) has completed, sponsored by Washington University Sc…