Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2023-11-28

Clinical Trial Update: Efficacy Study of Daily Administration of VPA in Patients Affected by Wolfram Syndrome [Phase 2]

View source ↗

Summary

Phase 2 trial update evaluating daily valproic acid (VPA) efficacy in patients with Wolfram Syndrome; status not disclosed.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: Centre d'Etude des Cellules Souches | Conditions: Wolfram Syndrome | Phase 2 | Status: UNKNOWN