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CLINICAL_TRIALS trial_result · 2026-04-14

Clinical Trial Update: AMX0035 in Adult Patients With Wolfram Syndrome [Phase 2]

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Summary

AMX0035 is being studied in a Phase 2 trial for adult patients with Wolfram syndrome, and the study is currently active but not recruiting.

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Diseases / indications

Drugs mentioned

  • AMX0035 (sodium phenylbutyrate and tauroursodeoxycholic acid)

Snippet

Sponsor: Amylyx Pharmaceuticals Inc. | Conditions: Wolfram Syndrome | Phase 2 | Status: ACTIVE_NOT_RECRUITING