Transfusion-dependent Beta-thalassemia
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CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Effects of Hydroxyurea and Metformin in Transfusion Dependent Beta-Thalassemia [Phase 4]
This clinical trial update describes a Phase 4 study evaluating hydroxyurea and metformin in transfusion-dependent beta-thalassemia, which h…
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CLINICAL_TRIALS trial_result · 2026-02-11Clinical Trial Update: Safety and Efficacy Evaluation of ET-01 Transplantation in Subjects With Transfusion Dependent β-Thalassaemia [NA]
The document reports the completion of a clinical trial evaluating ET-01 transplantation for safety and efficacy in transfusion-dependent be…
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CLINICAL_TRIALS trial_result · 2026-01-27Clinical Trial Update: Glucagon-Like Peptide 1 Receptor Agonist in Diabetes Mellitus Management in Children and Adolescents With Transfusion-Dependent Thalassemia [Phase 2]
A Phase 2 clinical trial evaluating a glucagon-like peptide-1 receptor agonist for diabetes management in children and adolescents with tran…
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CLINICAL_TRIALS trial_result · 2025-04-09Clinical Trial Update: Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy
This update provides long-term follow-up data for subjects with transfusion-dependent beta-thalassemia who were treated with an ex vivo gene…
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CLINICAL_TRIALS trial_result · 2025-04-02Clinical Trial Update: EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT) [Phase 1, Phase 2]
Editas Medicine reports an update for EDIT-301, an autologous hematopoietic stem cell gene-editing therapy, currently in Phase 1/Phase 2 for…
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CLINICAL_TRIALS trial_result · 2023-12-13Clinical Trial Update: A Study to Assess the Safety, Tolerability, and Efficacy of ST-400 for Treatment of Transfusion-Dependent Beta-thalassemia (TDT) [Phase 1, Phase 2]
A Phase 1/2 trial evaluating the safety, tolerability, and efficacy of ST-400 for transfusion-dependent beta-thalassemia has completed with …
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CLINICAL_TRIALS trial_result · 2016-12-12Clinical Trial Update: Effect of Deferasirox on Patients With Cardiac MRI T2* < 20 Msec [Phase 2]
Phase 2 trial evaluating Deferasirox in transfusion-dependent beta-thalassemia patients with myocardial iron overload (cardiac MRI T2* < 20 …