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CLINICAL_TRIALS ClinicalTrials.gov record update

A Multicenter Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Dose of Autologous Clustered Regularly Interspaced Short Palindromic Repeats Gene-edited Cluster of Differentiation 34 (CD34+) Human Hematopoietic Stem and Progenitor Cells (HSPC) (EDIT-301) in Transfusion-Dependent Beta Thalassemia (TDT)

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT05444894
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:26:39.964534+00:00
Published At
2025-04-02T00:00:00+00:00
Record Updated At
2025-04-02
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Transfusion Dependent Beta Thalassemia", "Hemoglobinopathies", "Thalassemia Major", "Thalassemia Intermedia"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2025-04-02"
protocolSection.identificationModule.nctId
"NCT05444894"
protocolSection.identificationModule.officialTitle
"A Multicenter Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Dose of Autologous Clustered Regularly Interspaced Short Palindromic Repeats Gene-edited Cluster of Differentiation 34 (CD34+) Human Hematopoietic Stem and Progenitor Cells (HSPC) (EDIT-301) in Transfusion-Dependent Beta Thalassemia (TDT)"
protocolSection.statusModule.overallStatus
"ACTIVE_NOT_RECRUITING"
protocolSection.designModule.phases
["PHASE1", "PHASE2"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • Transfusion Dependent Beta Thalassemia (protocolSection.conditionsModule.conditions)
  • Hemoglobinopathies (protocolSection.conditionsModule.conditions)
  • Thalassemia Major (protocolSection.conditionsModule.conditions)
  • Thalassemia Intermedia (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.