Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2025-04-09

Clinical Trial Update: Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy

View source ↗

Summary

This update provides long-term follow-up data for subjects with transfusion-dependent beta-thalassemia who were treated with an ex vivo gene therapy, reporting …

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Ex Vivo Gene Therapy for Transfusion-Dependent Beta-Thalassemia

Snippet

Sponsor: Genetix Biotherapeutics Inc. | Conditions: Transfusion-dependent Beta-Thalassemia | Status: ACTIVE_NOT_RECRUITING