Stargardt Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-07-31Clinical Trial Update: A Phase 2/3 Trial to Assess the Efficacy and Safety of OCU410ST for Stargardt Disease [Phase 2, Phase 3]
Phase 2/3 trial update for OCU410ST in Stargardt Disease indicating active status with ongoing efficacy and safety assessment.
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Oral Metformin for Treatment of ABCA4 Retinopathy [Phase 1, Phase 2]
An oral metformin trial for ABCA4 retinopathy and Stargardt disease is in Phase 1/Phase 2 and currently recruiting.
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Rod and Cone Mediated Function in Retinal Disease
Clinical trial registry entry for a study of rod and cone mediated function in retinal disease, sponsored by the National Eye Institute, cur…
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CLINICAL_TRIALS research · 2026-04-17Clinical Trial Update: A Study to Learn How Stargardt-type Eye Conditions Progress in Children and Adults
This clinical trial update describes a study led by Astellas Pharma Global Development to learn how Stargardt-type eye conditions progress i…
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CLINICAL_TRIALS research · 2026-04-16Clinical Trial Update: The Safety and Efficacy of ZVS106e in the Treatment of IRDs Caused by Biallelic Mutations in ABCA4 [EARLY_Phase 1]
Early-phase Phase 1 trial evaluating the safety and efficacy of ZVS106e for Stargardt disease caused by biallelic ABCA4 mutations; currently…
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety of a Single Intravitreal Injection of RTx-021 in Patients With Stargardt Disease [Phase 1, Phase 2]
A Phase 1/2 open-label dose-escalation trial to assess the safety of a single intravitreal injection of RTx-021 in patients with Stargardt d…
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CLINICAL_TRIALS research · 2026-04-09Clinical Trial Update: Study of ALK-001 on the Progression of Stargardt Disease [Phase 3]
Alkeus Pharmaceuticals reports that the Phase 3 trial of ALK-001 for Stargardt disease is currently recruiting. The study aims to evaluate d…
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CLINICAL_TRIALS research · 2026-04-06Clinical Trial Update: A Phase 2/3 Trial to Assess the Efficacy and Safety of OCU410ST for Stargardt Disease [Phase 2, Phase 3]
Ocugen's Phase 2/3 study of OCU410ST for Stargardt Disease is currently active but not recruiting.
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CLINICAL_TRIALS trial_result · 2026-04-02Clinical Trial Update: Restoration of Central Vision With PRIMA in Patients With Photoreceptor Degeneration [NA]
A clinical trial evaluating PRIMA for photoreceptor degeneration is currently recruiting, focusing on Stargardt disease and retinitis pigmen…
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CLINICAL_TRIALS research · 2026-03-31Clinical Trial Update: Development and Evaluation of Functional Visual Field and Navigation Endpoints in Moderate to Profound Inherited Retinal Disease (DEFINE-IRD)
Clinical trial update on the development and evaluation of functional visual field and navigation endpoints for moderate-to-profound inherit…
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CLINICAL_TRIALS trial_result · 2026-03-12Clinical Trial Update: Zimura Compared to Sham in Patients With Autosomal Recessive Stargardt Disease (STGD1) [Phase 2]
Phase 2 trial comparing Zimura to sham in autosomal recessive Stargardt disease (STGD1) completed; results have been posted.
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CLINICAL_TRIALS research · 2026-03-12Clinical Trial Update: A Phase 2/3 Study to Evaluate the Efficacy and Safety of Tinlarebant in Subjects With Stargardt Disease [Phase 2, Phase 3]
This clinical trial update reports a Phase 2/3 study evaluating tinlarebant for Stargardt disease (STGD1), with the trial currently active b…
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CLINICAL_TRIALS research · 2026-03-11Clinical Trial Update: Prescreening Study to Identify Potential Stargardt Participants for ACDN-01 Clinical Trials (STARPATH)
A prescreening study by Ascidian Therapeutics (STARPATH) to identify potential Stargardt disease participants for ACDN-01 clinical trials; r…
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CLINICAL_TRIALS research · 2026-03-09Clinical Trial Update: A Study of AAVB-039 in Participants With Stargardt Disease (STGD1) [Phase 1, Phase 2]
AAVantgarde Bio Srl is conducting a Phase 1/2 study of AAVB-039 in participants with Stargardt disease (STGD1), and the trial is currently r…
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: A Study of DC6001 Tablet in Healthy Chinese Adult Subjects [Phase 1]
Phase 1 study update of DC6001 Tablet in healthy Chinese adults; recruitment ongoing with Stargardt Disease listed as the condition.
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CLINICAL_TRIALS research · 2025-12-30Clinical Trial Update: Wide Field OCTA in Ocular Diseases
Clinical trial update on a wide-field optical coherence tomography angiography (OCTA) study across several ocular diseases, sponsored by IRC…
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CLINICAL_TRIALS research · 2025-12-11Clinical Trial Update: Safety and Preliminary Efficacy of VG801 in Patients With ABCA4 Mutation-associated Retinal Dystrophy (Stargardt Disease) [Phase 1, Phase 2]
Clinical trial update on VG801 for Stargardt disease due to ABCA4 mutations, reporting safety assessments and preliminary efficacy signals f…
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CLINICAL_TRIALS research · 2025-12-05Clinical Trial Update: Inherited Retinal Diseases: Natural History and Genotype-Phenotype Correlations
This clinical trial update describes inherited retinal diseases, focusing on natural history and genotype-phenotype correlations, with the s…
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CLINICAL_TRIALS research · 2025-12-02Clinical Trial Update: Study to Evaluate ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR) [Phase 1, Phase 2]
Phase 1/2 study evaluating ACDN-01 for ABCA4-related Stargardt retinopathy (STELLAR) is currently recruiting.
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CLINICAL_TRIALS trial_result · 2025-10-31Clinical Trial Update: Phase 3, Randomized, Placebo-Controlled Study of Tinlarebant to Explore Safety and Efficacy in Adolescent Stargardt Disease [Phase 3]
Phase 3 randomized, placebo-controlled study of tinlarebant in adolescents with Stargardt disease has completed, with safety and efficacy da…
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CLINICAL_TRIALS research · 2025-09-29Clinical Trial Update: The Effects of Disulfiram (Antabuse®) on Visual Acuity in Patients With Retinal Degeneration [Phase 1]
Phase 1 trial investigating the effects of disulfiram (Antabuse) on visual acuity in patients with retinal degeneration; the study is curren…
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CLINICAL_TRIALS research · 2025-09-19Clinical Trial Update: An Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene
An observational clinical trial is underway to track progression of Stargardt disease type 1 (STGD1) caused by bi-allelic ABCA4 mutations. T…
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CLINICAL_TRIALS research · 2025-09-18Clinical Trial Update: Feasibility and Tolerability Study of Smart Contact Lens With Healthy Subjects and Patients With Stargardt's Disease [NA]
This clinical trial update describes a feasibility and tolerability study of a smart contact lens in healthy subjects and patients with Star…
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CLINICAL_TRIALS research · 2025-08-28Clinical Trial Update: An Observational Study in Children and Adults With Stargardt Disease
An observational study enrolling children and adults with Stargardt disease is currently recruiting. The sponsor is AAVantgarde Bio Srl.
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CLINICAL_TRIALS research · 2025-08-27Clinical Trial Update: An Clinical Study Evaluating the Safety, Tolerability, and efficAcy of HG005 in StaRgardT Disease [EARLY_Phase 1]
This clinical trial update notes a Phase 1 study evaluating the safety, tolerability, and efficacy of HG005 for Stargardt disease, Type 1, c…