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CLINICAL_TRIALS research · 2025-09-19

Clinical Trial Update: An Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene

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Summary

An observational clinical trial is underway to track progression of Stargardt disease type 1 (STGD1) caused by bi-allelic ABCA4 mutations. The study is currentl…

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Diseases / indications

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Sponsor: Splice Bio | Conditions: Stargardt, Stargardt's Disease | Status: RECRUITING