CLINICAL_TRIALS
research
· 2025-09-19
Clinical Trial Update: An Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene
Summary
An observational clinical trial is underway to track progression of Stargardt disease type 1 (STGD1) caused by bi-allelic ABCA4 mutations. The study is currentl…
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Diseases / indications
Snippet
Sponsor: Splice Bio | Conditions: Stargardt, Stargardt's Disease | Status: RECRUITING