Stargardt Disease
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CLINICAL_TRIALS research · 2025-06-29Clinical Trial Update: ABCA4-associated Disease in Childhood and Adolescence - a Phenotype Study
This update notes the completion of a phenotype-focused clinical trial examining ABCA4-associated disease in children and adolescents. The s…
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CLINICAL_TRIALS trial_result · 2025-06-12Clinical Trial Update: Phase I/II Follow-up Study of SAR422459 in Patients With Stargardt's Macular Degeneration [Phase 2]
A Phase II follow-up study of SAR422459 for Stargardt disease is currently active but not recruiting, sponsored by Sanofi.
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CLINICAL_TRIALS research · 2025-04-29Clinical Trial Update: A Phase 1/2, First-in-Human Dose Escalation/Expansion Study to Evaluate the Safety, Tolerability and Preliminary Efficacy of a Subretinal Injection of SB-007 in Subjects With Stargardt Disease (STGD1) [Phase 1, Phase 2]
A Phase 1/2 first-in-human study is evaluating SB-007 delivered by subretinal injection in Stargardt disease (STGD1), assessing safety, tole…
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CLINICAL_TRIALS trial_result · 2025-04-27Clinical Trial Update: Phase 2 Tolerability and Effects of ALK-001 on Stargardt Disease [Phase 2]
Phase 2 trial evaluating tolerability and effects of ALK-001 in Stargardt disease. The study is currently enrolling by invitation.
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CLINICAL_TRIALS trial_result · 2025-04-27Clinical Trial Update: Phase 1 Safety Study of ALK-001 in Healthy Volunteers [Phase 1]
Phase 1 safety study of ALK-001 in healthy volunteers has completed, assessing safety in humans. It targets retinal degenerative conditions …
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CLINICAL_TRIALS research · 2025-04-27Clinical Trial Update: Open-Label Extension: Tolerability and Effects of ALK-001 on Stargardt Disease (TEASE) [Phase 2]
An open-label extension of ALK-001 in Stargardt disease (TEASE) is a Phase 2 study evaluating tolerability and effects; the trial is current…
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CLINICAL_TRIALS trial_result · 2025-04-22Clinical Trial Update: Function and Imaging Assessments for G1961E-associated Stargardt Disease
This clinical trial update discusses function and imaging assessments for Stargardt disease associated with the ABCA4 G1961E variant, noting…
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CLINICAL_TRIALS research · 2025-04-22Clinical Trial Update: High Resolution Retinal Imaging
A University of Pennsylvania-sponsored clinical trial using high-resolution retinal imaging is currently recruiting participants for several…
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CLINICAL_TRIALS research · 2025-03-27Clinical Trial Update: Inherited Retinal Degenerative Disease Registry
A Foundation Fighting Blindness–sponsored inherited retinal degenerative disease registry is currently recruiting participants to collect in…
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CLINICAL_TRIALS research · 2025-03-24Clinical Trial Update: A Prospective Observational Study to Assess the Reliability and Validity of the MLSDT
A prospective observational study to assess the reliability and validity of the MLSDT for macular degeneration-related conditions, currently…
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CLINICAL_TRIALS research · 2025-03-24Clinical Trial Update: Non-interventional Long Term Follow-up Study of Participants Previously Enrolled in the STARLIGHT Study
A non-interventional long-term follow-up study is ongoing for participants previously enrolled in the STARLIGHT study for Stargardt disease.
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CLINICAL_TRIALS research · 2025-03-20Clinical Trial Update: Stem Cell Ophthalmology Treatment Study II [NA]
The clinical trial update indicates that the Stem Cell Ophthalmology Treatment Study II is currently recruiting for multiple retinal and opt…
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CLINICAL_TRIALS research · 2025-01-08Clinical Trial Update: Observational Study to Assess Endpoint Operational Feasibility & Measurement Properties in Patients with Retinal Degeneration
This clinical trial update describes an observational study to assess endpoint feasibility and measurement properties in patients with retin…
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CLINICAL_TRIALS trial_result · 2024-10-31Clinical Trial Update: Sub-retinal Transplantation of hESC Derived RPE(MA09-hRPE)Cells in Patients With Stargardt's Macular Dystrophy [Phase 1, Phase 2]
Astellas Institute for Regenerative Medicine conducted a Phase 1/2 study evaluating sub-retinal transplantation of MA09-hRPE cells for Starg…
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CLINICAL_TRIALS trial_result · 2024-10-31Clinical Trial Update: Safety and Tolerability of Sub-retinal Transplantation of Human Embryonic Stem Cell Derived Retinal Pigmented Epithelial (hESC-RPE) Cells in Patients With Stargardt's Macular Dystrophy (SMD) [Phase 1, Phase 2]
This Phase 1/2 trial evaluated the safety and tolerability of sub-retinal transplantation of human embryonic stem cell–derived retinal pigme…
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CLINICAL_TRIALS trial_result · 2024-10-31Clinical Trial Update: Long Term Follow Up of Sub-retinal Transplantation of hESC Derived RPE Cells in Stargardt Macular Dystrophy Patients
Long-term follow-up results are reported for sub-retinal transplantation of human embryonic stem cell-derived retinal pigment epithelium cel…
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CLINICAL_TRIALS trial_result · 2024-04-12Clinical Trial Update: This is a Dose-finding Study Followed by 2-year Extension Study to Evaluate Safety and Tolerability of Tinlarebant in Adolescent Subjects With Stargardt Disease [Phase 1, Phase 2]
Phase 1/2 dose-finding and 2-year extension study evaluating the safety and tolerability of tinlarebant in adolescents with Stargardt diseas…
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CLINICAL_TRIALS trial_result · 2024-03-08Clinical Trial Update: Safety and Efficacy of a Single Subretinal Injection of JWK006 Gene Therapy in Subjects With Stargardt Disease(STGD1) [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating safety and efficacy of a single subretinal injection of JWK006 gene therapy for Stargardt Disease (STG…
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CLINICAL_TRIALS trial_result · 2023-11-09Clinical Trial Update: Safety and Effects of a Single Intravitreal Injection of vMCO-010 Optogenetic Therapy in Subjects With Stargardt Disease [Phase 2]
Phase 2 trial update on safety and effects of a single intravitreal injection of vMCO-010 optogenetic therapy in Stargardt disease.
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CLINICAL_TRIALS trial_result · 2023-08-03Clinical Trial Update: Safety and Efficacy of Emixustat in Stargardt Disease [Phase 3]
Phase 3 results report the safety and efficacy of Emixustat for Stargardt disease; the trial has completed and results were posted.
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CLINICAL_TRIALS trial_result · 2021-04-27Clinical Trial Update: Pharmacodynamic Study of Emixustat Hydrochloride in Subjects With Macular Atrophy Secondary to Stargardt Disease [Phase 2]
Phase 2 pharmacodynamic study of emixustat hydrochloride in Stargardt disease–related macular atrophy completed with posted results.
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CLINICAL_TRIALS trial_result · 2021-04-27Clinical Trial Update: Study of STG-001 in Subjects With Stargardt Disease [Phase 2]
Phase 2 clinical trial study of STG-001 in Stargardt Disease has completed.
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CLINICAL_TRIALS research · 2020-07-22Clinical Trial Update: Stem Cell Therapy for Outer Retinal Degenerations [Phase 1, Phase 2]
A completed early-stage trial investigating stem cell therapy for age-related macular degeneration and Stargardt's disease.
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CLINICAL_TRIALS trial_result · 2020-06-05Clinical Trial Update: Phase I/IIA Study of SAR422459 in Participants With Stargardt's Macular Degeneration [Phase 1, Phase 2]
Phase I/IIA trial of SAR422459 for Stargardt's disease was terminated with results posted in 2020.
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CLINICAL_TRIALS trial_result · 2020-04-01Clinical Trial Update: Efficacy of Acupuncture in Macular Diseases [NA]
A completed clinical trial evaluating acupuncture for macular diseases (age-related macular degeneration and Stargardt disease) with results…