Records containing: Spinal Muscular Atrophy
This is the wording recorded or indexed by the source. An agency index term is not necessarily an authorised indication. Co-listed drug names are not linked to this term as a treatment relationship.
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CLINICAL_TRIALS study record update · 2026-04-23The Feasibility of Virtual Reality in Children With Neuromuscular Disease and the Effectiveness of Virtual Reality and Biofeedback Training on Functional Levels of Children With Neuromuscular Disease
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CLINICAL_TRIALS study record update · 2026-04-23The Impact of Developmental Support Provided to Mothers of 12-36 Month Old Babies Diagnosed With Spinal Muscular Atrophy (SMA) on Infant Development and Mothers' Developmental Knowledge
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CLINICAL_TRIALS study record update · 2026-04-21An Open-Label, Phase 3 Study to Evaluate the Efficacy and Safety of Salanersen (BIIB115) in Participants Aged 15-60 Years With Spinal Muscular Atrophy Who Are Either Treatment-Naïve or Have Previously Been Treated With Risdiplam
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CLINICAL_TRIALS study record update · 2026-04-20Long-term Follow-up Study of Patients With Spinal Muscular Atrophy Receiving Risdiplam Treatment
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CLINICAL_TRIALS study record update · 2026-04-16Safety and Performance of the ThecaFlex DRx™ System Port and Catheter for Chronic Intrathecal Access, Cerebrospinal Fluid (CSF) Aspiration, and DElivery of Nusinersen in Spinal Muscular Atrophy (SMA) Patients Resistant to Lumbar PunctuRE Trial (PIERRE)
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CLINICAL_TRIALS study record update · 2026-04-13A Phase 2, Randomised, Double-blind, Placebo-controlled, 2-way Crossover Study to Evaluate the Efficacy, Safety, and Tolerability of NMD670 in Ambulatory Adults With Type 3 Spinal Muscular Atrophy
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CLINICAL_TRIALS study record update · 2026-03-25A Phase 2, Double-Blind Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Efficacy, and Safety of Apitegromab in Subjects <2 Years Old With Spinal Muscular Atrophy (SMA)
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CLINICAL_TRIALS study record update · 2026-03-18Onasemnogene Abeparvovec: ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
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CLINICAL_TRIALS study record update · 2026-03-17Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults withNeuromuscular Disease
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CLINICAL_TRIALS study record update · 2026-02-23Investigating NMJ Defects in SMA Following Central and Peripheral SMN Restoration
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CLINICAL_TRIALS study record update · 2026-02-23The Role of Motor Unit Number Estimation (MUNE) in Adults With Spinal Muscular Atrophy (SMA)
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CLINICAL_TRIALS study record update · 2026-02-05Characterizing Perceived Physical Fatigability in Nusinersen-treated Adolescents and Adults: The SMA EFFORT
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CLINICAL_TRIALS study record update · 2026-02-04A Randomized, Double-Blind, Placebo-Controlled, Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Ambulatory and Non-Ambulatory Participants With Spinal Muscular Atrophy With Open-Label Extension
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CLINICAL_TRIALS study record update · 2026-01-30Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy
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CLINICAL_TRIALS study record update · 2026-01-22Phase 3, Double-Blind, Placebo-Controlled Trial to Evaluate the Efficacy and Safety of Apitegromab (SRK-015) in Patients With Later-Onset Spinal Muscular Atrophy Receiving Background Nusinersen or Risdiplam Therapy
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CLINICAL_TRIALS study record update · 2025-12-23Assessment of Motor Development Related to Use of Orthoses in SMA II and III
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CLINICAL_TRIALS study record update · 2025-12-10Implementation of Flexible Endoscopic Evaluation of Swallowing (FEES) and Standardized FEES Scores in the Diagnostic Work-up of Dysphagia in Spinal Muscular Atrophy - DYS-SMA Trial
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CLINICAL_TRIALS study record update · 2025-12-03A Multicenter, Interventional, Open-label Study to Monitor the Evolution of Motor Function in SMA Type II Adults Patients Treated With SPINRAZA®
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CLINICAL_TRIALS study record update · 2025-12-03Mechanisms and Treatment of Exercise Intolerance and Persistent Fatigue in Spinal Muscular Atrophy
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CLINICAL_TRIALS study record update · 2025-11-17CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain
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CLINICAL_TRIALS study record update · 2025-11-04Pilot Study Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
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CLINICAL_TRIALS study record update · 2025-10-20An Open-Label Study to Assess the Efficacy, Safety, Tolerability, and Pharmacokinetics of Multiple Doses of ISIS 396443 Delivered Intrathecally to Subjects With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
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CLINICAL_TRIALS study record update · 2025-10-01An Open-Label Study to Investigate the Safety, Tolerability, and Pharmacokinetics/Pharmacodynamics of Risdiplam (RO7034067) in Adult and Pediatric Patients With Spinal Muscular Atrophy
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CLINICAL_TRIALS study record update · 2025-09-15Quantification of Motor Function in Infants With Spinal Muscular Atrophy Treated With Innovative Therapies, IMUSMA Project
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CLINICAL_TRIALS study record update · 2025-09-15Pediatric Powered Wheelchair Standing Devices: An Exploratory Study