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CLINICAL_TRIALS research · 2026-02-05

Clinical Trial Update: Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

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Summary

A new clinical trial is recruiting to characterize perceived physical fatigability in individuals with spinal muscular atrophy treated with nusinersen.

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Diseases / indications

Drugs mentioned

  • Spinraza (nusinersen)

Snippet

Sponsor: Columbia University | Conditions: Spinal Muscular Atrophy | Status: RECRUITING