CLINICAL_TRIALS
research
· 2025-11-04
Clinical Trial Update: Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
Summary
This clinical trial update describes ongoing recruitment for a study assessing physiologic, pharmacodynamic, and clinical skeletal muscle responses in spinal mu…
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Snippet
Sponsor: St. Jude Children's Research Hospital | Conditions: Spinal Muscular Atrophy | Status: RECRUITING