Clinical Trial Update: Investigating NMJ Defects in SMA Following Central and Peripheral SMN Restoration

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Summary

A completed clinical trial studying neuromuscular junction defects in spinal muscular atrophy following restoration of SMN protein in central and peripheral ner…

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Diseases / indications

• Spinal Muscular Atrophy

Snippet

Sponsor: Bakri Elsheikh | Conditions: Spinal Muscular Atrophy | Status: COMPLETED