Sickle Cell Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-11-18Clinical Trial Update: Study to Assess the Effect of Long-term Treatment With Voxelotor in Participants Who Have Completed Treatment in Study GBT440-031 [Phase 3]
A Phase 3 extension study evaluating long-term treatment with voxelotor in participants who completed the prior study in sickle cell disease…
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CLINICAL_TRIALS research · 2025-11-18Clinical Trial Update: Collect of Cord Blood From Subjects at Risk for Sickle Cell Disease, for the Purpose of Laboratory Research
A completed clinical trial from France collected cord blood from subjects at risk for sickle cell disease for laboratory research.
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CLINICAL_TRIALS research · 2025-11-14Clinical Trial Update: Integrative Training Program for Pediatric Sickle Cell Pain [NA]
Emory University is recruiting for a clinical trial evaluating an integrative training program to support pediatric sickle cell disease pain…
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CLINICAL_TRIALS research · 2025-11-14Clinical Trial Update: Gene Editing For Sickle Cell Disease [Phase 1]
A Phase 1 clinical trial led by St. Jude Children's Research Hospital is evaluating a gene editing approach for sickle cell disease and is c…
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CLINICAL_TRIALS trial_result · 2025-11-13Clinical Trial Update: Open-Label Extension of Voxelotor [Phase 3]
Open-label extension of voxelotor in sickle cell disease (Phase 3) has been terminated, with results posted.
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CLINICAL_TRIALS trial_result · 2025-11-12Clinical Trial Update: Long - Term Follow Up of Sickle Cell Disease and Beta-thalassemia Subjects Previously Exposed to BIVV003 or ST-400.
Sangamo Therapeutics provides an update on long-term follow-up for sickle cell disease and beta-thalassemia subjects previously treated with…
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CLINICAL_TRIALS research · 2025-11-12Clinical Trial Update: Cutaneous Hydration Assessment in SCD [NA]
This clinical trial update notes an ongoing study evaluating cutaneous hydration in people with Sickle Cell Disease. The trial is currently …
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CLINICAL_TRIALS research · 2025-11-10Clinical Trial Update: Peripheral Arterial Tonometry and Neurocognition in Sickle Cell Disease
A St. Jude-sponsored clinical study on peripheral arterial tonometry and neurocognition in people with sickle cell disease is currently recr…
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CLINICAL_TRIALS research · 2025-11-04Clinical Trial Update: Investigation of the Genetics of Hematologic Diseases
A St. Jude-sponsored clinical trial update indicates a study on the genetics of hematologic diseases is currently recruiting, covering sever…
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EMA approval · 2025-11-03EMA Authorised: Xromi (hydroxycarbamide) — Lipomed GmbH
The EMA authorised Xromi, a hydroxycarbamide medicine from Lipomed GmbH, for indications in anemia and sickle cell disease.
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CLINICAL_TRIALS trial_result · 2025-10-28Clinical Trial Update: The Feasibility of the PAINReportIt Guided Relaxation Intervention-INPATIENT [NA]
A completed inpatient feasibility study evaluating the PAINReportIt guided relaxation intervention for pain management in sickle cell diseas…
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CLINICAL_TRIALS trial_result · 2025-10-27Clinical Trial Update: Pharmacokinetics, Pharmacodynamics and Safety of Epeleuton in Patients With Sickle Cell Disease [Phase 2]
Phase 2 clinical trial update evaluating the pharmacokinetics, pharmacodynamics, and safety of Epeleuton in patients with Sickle Cell Diseas…
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CLINICAL_TRIALS trial_result · 2025-10-27Clinical Trial Update: Gerofit Exercise Intervention for Older Adults With Sickle Cell Disease (SICKLE-FIT Study) [NA]
The SICKLE-FIT trial, evaluating the Gerofit exercise intervention for older adults with sickle cell disease, has completed.
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FDA approval · 2025-10-21FDA Approved: DEFERASIROX — Supplemental Application (Actavis Pharma, Inc.)
FDA approved a supplemental application for Deferasirox from Actavis Pharma, Inc. This action updates the regulatory status of the product.
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CLINICAL_TRIALS research · 2025-10-20Clinical Trial Update: Integrative Medicine in Pain Management in Sickle Cell Disease, 2.0 [NA]
Indiana University is recruiting for a study on integrative medicine approaches to pain management in sickle cell disease, including acupunc…
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EMA withdrawal · 2025-10-17EMA confirms suspension of sickle cell disease medicine Oxbryta
EMA has suspended Oxbryta (voxelotor) for sickle cell disease after trials showed a higher rate of death and disease complications, so the b…
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CLINICAL_TRIALS research · 2025-10-16Clinical Trial Update: Integrative Medicine in Pain Management in Sickle Cell Disease [NA]
Indiana University is conducting an integrative medicine trial to manage pain in sickle cell disease; the study is currently active but not …
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CLINICAL_TRIALS research · 2025-10-14Clinical Trial Update: Early Screening and Treatment of Heart Complication in Sickle Cell Disease [Phase 2]
A Phase 2 clinical trial by Inova Health Care Services is evaluating early screening and treatment of heart complications in patients with s…
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CLINICAL_TRIALS trial_result · 2025-10-10Clinical Trial Update: A Research Study of the Effect of Food on Etavopivat in Healthy Participants [Phase 1]
Phase 1 study assessing the effect of food on Etavopivat in healthy participants has been completed; the update focuses on pharmacokinetic i…
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CLINICAL_TRIALS research · 2025-10-09Clinical Trial Update: Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)
This clinical trial update describes a needs-assessment–driven program to develop decision aids for gene therapy in rare diseases (GENETX), …
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CLINICAL_TRIALS trial_result · 2025-10-08Clinical Trial Update: Interest of Famotidine in Children With Sickle Cell Disease [Phase 2, Phase 3]
Completed Phase 2/Phase 3 clinical trial evaluating famotidine for sickle cell disease in children.
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CLINICAL_TRIALS trial_result · 2025-10-03Clinical Trial Update: Long-term Follow-up (LTFU) of Patients Treated With Genome-edited Autologous Hematopoietic Stem and Progenitor Cells (HSPC) [Phase 1]
This clinical trial update provides long-term follow-up results for sickle cell disease patients treated with genome-edited autologous hemat…
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CLINICAL_TRIALS research · 2025-10-03Clinical Trial Update: Integrative Diagnosis for SCD and Other RADs
An ongoing clinical trial focused on integrative diagnosis for sickle cell disease and related red blood cell disorders, currently recruitin…
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CLINICAL_TRIALS trial_result · 2025-10-02Clinical Trial Update: Adding Azathioprine/Hydroxyurea Preconditioning to Alemtuzumab/TBI to Reduce Risk of Graft Failure in MSD HSCT in Adult SCD Patients
This clinical trial update notes the addition of azathioprine and hydroxyurea preconditioning to an alemtuzumab/TBI regimen in matched-sibli…
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CLINICAL_TRIALS research · 2025-10-02Clinical Trial Update: Cannabinoids for the Reduction of Inflammation and Sickle Cell Related Pain [Phase 2]
Phase 2 clinical trial sponsored by Icahn School of Medicine at Mount Sinai is evaluating cannabinoids to reduce inflammation and sickle cel…