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CLINICAL_TRIALS trial_result · 2025-08-11

Clinical Trial Update: A Safety and Efficacy Study Evaluating CTX001 in Subjects With Severe Sickle Cell Disease [Phase 2, Phase 3]

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Summary

A safety and efficacy study of CTX001 in subjects with severe Sickle Cell Disease has completed Phase 2 and Phase 3 trials.

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Diseases / indications

Drugs mentioned

  • CTX001

Snippet

Sponsor: Vertex Pharmaceuticals Incorporated | Conditions: Sickle Cell Disease, Hematological Diseases | Phase 2, Phase 3 | Status: COMPLETED