CLINICAL_TRIALS
trial_result
· 2025-08-11
Clinical Trial Update: A Safety and Efficacy Study Evaluating CTX001 in Subjects With Severe Sickle Cell Disease [Phase 2, Phase 3]
Summary
A safety and efficacy study of CTX001 in subjects with severe Sickle Cell Disease has completed Phase 2 and Phase 3 trials.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Vertex Pharmaceuticals Incorporated | Conditions: Sickle Cell Disease, Hematological Diseases | Phase 2, Phase 3 | Status: COMPLETED