Combined Immunodeficiency

• CLINICAL_TRIALS trial_result · 2008-03-04
  Clinical Trial Update: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study

  This document reports a completed natural history study of a gene transfer therapy for ADA-deficiency-associated severe combined immunodefic…

• CLINICAL_TRIALS trial_result · 2008-01-24
  Clinical Trial Update: Gene Therapy for ADA-SCID [Phase 1, Phase 2]

  A Phase 1/2 gene therapy trial for ADA-SCID conducted by IRCCS San Raffaele has completed.