Clinical Trial Update: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study

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Summary

This document reports a completed natural history study of a gene transfer therapy for ADA-deficiency-associated severe combined immunodeficiency. The trial (NC…

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Diseases / indications

• Combined Immunodeficiency

Snippet

Sponsor: National Human Genome Research Institute (NHGRI) | Conditions: Severe Combined Immunodeficiency | Status: COMPLETED