Combined Immunodeficiency
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS withdrawal · 2025-12-01Clinical Trial Update: Matched Related and Unrelated Donor Stem Cell Transplantation for Severe Combined Immune Deficiency (SCID): Busulfan-based Conditioning With h-ATG, Radiation, and Sirolimus [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating busulfan-based conditioning with h-ATG, radiation, and sirolimus for matched related/unrelated donor s…
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CLINICAL_TRIALS withdrawal · 2015-12-03Clinical Trial Update: Sirolimus Prophylaxis for aGVHD in TME SCID [Phase 2]
A Phase 2 trial evaluating sirolimus prophylaxis for acute graft-versus-host disease in Severe Combined Immunodeficiency with transplacental…