Records containing: Rett Syndrome
This is the wording recorded or indexed by the source. An agency index term is not necessarily an authorised indication. Co-listed drug names are not linked to this term as a treatment relationship.
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CLINICAL_TRIALS study record update · 2026-03-31A Phase 3 Randomized, Double-Blind, Placebo Controlled, Parallel Group, Multicenter Study With Open-Label Extension to Evaluate the Efficacy And Safety of Fenfluramine Hydrochloride in Study Participants With Rett Syndrome
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CLINICAL_TRIALS study record update · 2026-03-27A Randomized, Double-Blind, Placebo-Controlled, Parallel-Group Phase 3 Study of Bionetide for the Treatment of Girls and Women With Rett Syndrome
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CLINICAL_TRIALS study record update · 2026-03-18ASPIRE Study: A Multicenter, Open-Label Study to Evaluate the Safety, Tolerability, and Preliminary Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy, for the Treatment of Pediatric Females Aged >2 to <4 Years With Rett Syndrome
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CLINICAL_TRIALS study record update · 2026-03-13A Baseline-Controlled, Open-Label, Multicenter, Single-Arm, Pivotal Study to Evaluate the Efficacy, Safety, and Tolerability of NGN-401 in Subjects With Rett Syndrome (Embolden)
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CLINICAL_TRIALS study record update · 2026-02-20Technology-supported Motor Rehabilitation for People With Rett Syndrome (TeMoRett) Sub-project: Psychophysiological Personalization of the Technology-supported Motor Rehabilitation for People With Rett Syndrome
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CLINICAL_TRIALS study record update · 2026-02-17The Rett Syndrome Global Registry
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CLINICAL_TRIALS study record update · 2026-01-23Promoting Prosocial Behavior in Syndromic Intellectual and Developmental Disabilities
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CLINICAL_TRIALS study record update · 2025-12-30An Open-label Phase 1/2/3 Study Consisting of a Phase 1/2 Safety and Dose-escalation and Phase 3 Dose-expansion Study to Evaluate Safety and Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy in Females With Rett Syndrome
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CLINICAL_TRIALS study record update · 2025-12-19Validation of Innovative Biosensors for Rett Autonomic Symptom Tracking
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CLINICAL_TRIALS study record update · 2025-12-02A Phase II/III Double-blind, Randomised, Placebo-controlled, Crossover Study Investigating the Efficacy and Safety of NTI164 in Children and Young Adults With Rett Syndrome
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CLINICAL_TRIALS study record update · 2025-10-20Characterization of Translatable Neurophysiological Biomarkers to Enhance Therapeutic Development in Rett Syndrome
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CLINICAL_TRIALS study record update · 2025-10-15A Multicenter, Open Label, Randomized, Dose-Escalation and Dose-Expansion Study of the Safety, Tolerability, and Efficacy of a Single Intrathecal Administration of TSHA-102, an AAV9-Delivered Gene Therapy, for the Treatment of Pediatric Females With Rett Syndrome
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CLINICAL_TRIALS study record update · 2025-09-03Obi Medical Robot: Evaluating Effectiveness Related to Usability in Providers, Caregivers & Patients
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CLINICAL_TRIALS study record update · 2025-09-02Rett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett Syndrome Using an "N of 1" Study Design
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CLINICAL_TRIALS study record update · 2025-08-20Personalized MECP2 Gene Therapy Using CRISPR/Cas9 Technology Coupled to AAV-mediated Delivery in 3D Cell Culture and KI Mice
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CLINICAL_TRIALS study record update · 2025-07-31Piloting an Early Intervention Program for Infants With Rare Neurogenetic Disorders
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CLINICAL_TRIALS study record update · 2025-07-16A Pilot Study of an Antioxidant Cocktail vs. Placebo in the Treatment of Children and Adolescents With Rett Syndrome
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CLINICAL_TRIALS study record update · 2025-07-01Study on the Safety, Tolerability, and Preliminary Efficacy of Single Intrathecal Injection of AAV-MECP2 in the Treatment of Rett Syndrome
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CLINICAL_TRIALS study record update · 2025-06-12Cognitive Function in Rett Syndrome During Trofinetide Treatment
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CLINICAL_TRIALS study record update · 2025-04-04Early Check: A Collaborative Innovation to Facilitate Pre-Symptomatic Clinical Trials in Newborns
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CLINICAL_TRIALS study record update · 2025-02-27A Randomized, Double-Blind, Placebo-Controlled, Phase 2/ Phase 3 Study of NA-921 (Bionetide) for the Treatment of Girls and Women with Rett Syndrome
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CLINICAL_TRIALS study record update · 2025-02-18An Exploratory Trial of Esketamine for the Treatment of Rett Syndrome
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CLINICAL_TRIALS study record update · 2024-11-14Assessing Emerald and MC10 nPoint Biosensors for Rett Syndrome
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CLINICAL_TRIALS study record update · 2024-10-03Assessing the Effectiveness of Customized Computer Activities on Reducing Stereotypies and Improving Independent Upper Extremity Motor Skills in Persons with Rett Syndrome
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CLINICAL_TRIALS study record update · 2024-10-01Assessing the Safety and Efficacy of Full-Spectrum Medicinal Cannabis Plant Extract 0.08% THC (NTI164) in the Treatment of Rett Syndrome (RTT)